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- [1] Efficacy of Eculizumab in Coexisting Complement C3 Glomerulopathy and Atypical Hemolytic Uremic SyndromeKIDNEY INTERNATIONAL REPORTS, 2021, 6 (02): : 534 - 537论文数: 引用数: h-index:机构:Diomedi-Camassei, Francesca论文数: 0 引用数: 0 h-index: 0机构: IRCCS Osped Pediat Bambino Gest, Pathol Unit, Dept Labs, Rome, Italy IRCCS Osped Pediat Bambino Gest, Div Nephrol, Dept Pediat Subspecialties, Rome, ItalyDonadelli, Roberta论文数: 0 引用数: 0 h-index: 0机构: Res Inst Mario Negri IRCCS, Clin Res Ctr Rare Dis Aldo & Cele Dacco & Ctr Ann, Sci & Technol Pk Kilometro Rosso, Bergamo, Italy IRCCS Osped Pediat Bambino Gest, Div Nephrol, Dept Pediat Subspecialties, Rome, ItalyMele, Caterina论文数: 0 引用数: 0 h-index: 0机构: Res Inst Mario Negri IRCCS, Clin Res Ctr Rare Dis Aldo & Cele Dacco & Ctr Ann, Sci & Technol Pk Kilometro Rosso, Bergamo, Italy IRCCS Osped Pediat Bambino Gest, Div Nephrol, Dept Pediat Subspecialties, Rome, ItalyEmma, Francesco论文数: 0 引用数: 0 h-index: 0机构: IRCCS Osped Pediat Bambino Gest, Div Nephrol, Dept Pediat Subspecialties, Rome, Italy IRCCS Osped Pediat Bambino Gest, Div Nephrol, Dept Pediat Subspecialties, Rome, ItalyVivarelli, Marina论文数: 0 引用数: 0 h-index: 0机构: IRCCS Osped Pediat Bambino Gest, Div Nephrol, Dept Pediat Subspecialties, Rome, Italy IRCCS Osped Pediat Bambino Gest, Div Nephrol, Dept Pediat Subspecialties, Rome, Italy
- [2] Mutations in complement C3 predispose to development of atypical hemolytic uremic syndromeBLOOD, 2008, 112 (13) : 4948 - 4952Fremeaux-Bacchi, Veronique论文数: 0 引用数: 0 h-index: 0机构: Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, France Cordeliers Res Ctr, INSERM, UMRS 872, Paris, France Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceMiller, Elizabeth C.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, Div Rheumatol, St Louis, MO USA Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceLiszewski, M. Kathryn论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, Div Rheumatol, St Louis, MO USA Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceStrain, Lisa论文数: 0 引用数: 0 h-index: 0机构: Newcastle Tyne Hosp, Natl Hlth Serv Fdn Trust, No Mol Genet Serv, Newcastle Upon Tyne, Tyne & Wear, England Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceBlouin, Jacques论文数: 0 引用数: 0 h-index: 0机构: Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, France Cordeliers Res Ctr, INSERM, UMRS 872, Paris, France Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceBrown, Alison L.论文数: 0 引用数: 0 h-index: 0机构: Newcastle Tyne Hosp, Natl Hlth Serv Fdn Trust, Dept Renal Med, Newcastle Upon Tyne, Tyne & Wear, England Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceMoghal, Nadeem论文数: 0 引用数: 0 h-index: 0机构: Newcastle Tyne Hosp, Natl Hlth Serv Fdn Trust, Dept Paediat Nephrol, Newcastle Upon Tyne, Tyne & Wear, England Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceKaplan, Bernard S.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Nephrol, Philadelphia, PA USA Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceWeiss, Robert A.论文数: 0 引用数: 0 h-index: 0机构: Maria Fareri Childrens Hosp, Westchester Med Ctr, Valhalla, NY USA Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceLhotta, Karl论文数: 0 引用数: 0 h-index: 0机构: Univ Innsbruck Hosp, Dept Internal Med, Div Clin Nephrol, A-6020 Innsbruck, Austria Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceKapur, Gaurav论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Michigan, Detroit, MI 48201 USA Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceMattoo, Tej论文数: 0 引用数: 0 h-index: 0机构: Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceNivet, Hubert论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Tours, Unite Nephrol Pediat, Tours, France Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceWong, William论文数: 0 引用数: 0 h-index: 0机构: Starship Childrens Hosp, Auckland, New Zealand Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceGie, Sophie论文数: 0 引用数: 0 h-index: 0机构: CHU Rennes, Dept Med Enfant & Adolescent, Hop Sud, Rennes, France Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, Francede Ligny, Bruno Hurault论文数: 0 引用数: 0 h-index: 0机构: Hop Clemenceau, Serv Nephrol Transplantat Renale, Caen, France Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceFischbach, Michel论文数: 0 引用数: 0 h-index: 0机构: Hop Hautepierre, Serv Pediat, Strasbourg, France Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceGupta, Ritu论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, Div Rheumatol, St Louis, MO USA Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceHauhart, Richard论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, Div Rheumatol, St Louis, MO USA Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceMeunier, Vincent论文数: 0 引用数: 0 h-index: 0机构: Hop Robert Boulin, Serv Med Interne, Libourne, France Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceLoirat, Chantal论文数: 0 引用数: 0 h-index: 0机构: Hop Robert Debre, Serv Nephrol Pediat, F-75019 Paris, France Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceDragon-Durey, Marie-Agnes论文数: 0 引用数: 0 h-index: 0机构: Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, France Cordeliers Res Ctr, INSERM, UMRS 872, Paris, France Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceFridman, Wolf H.论文数: 0 引用数: 0 h-index: 0机构: Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, France Cordeliers Res Ctr, INSERM, UMRS 872, Paris, France Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceJanssen, Bert J. C.论文数: 0 引用数: 0 h-index: 0机构: Univ Utrecht, Bijvoet Ctr Biomol Res, Fac Sci, Utrecht, Netherlands Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceGoodship, Timothy H. J.论文数: 0 引用数: 0 h-index: 0机构: Univ Newcastle, Inst Human Genet, Newcastle Upon Tyne, Tyne & Wear, England Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, FranceAtkinson, John P.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, Div Rheumatol, St Louis, MO USA Hop Europeen Georges Pompidou, Serv Immunol Biol, F-75908 Paris 15, France
- [3] Complement C3 mutation causing atypical hemolytic uremic syndrome successfully treated with eculizumabHEMATOLOGY TRANSFUSION AND CELL THERAPY, 2021, 43 (03) : 364 - 367论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Bleeker, Jonathan论文数: 0 引用数: 0 h-index: 0机构: Univ South Dakota, Sanford Sch Med, Sioux Falls, SD 57105 USA Univ South Dakota, Sanford Sch Med, Sioux Falls, SD 57105 USA
- [4] Mutations of C3 in Atypical Hemolytic Uremic Syndrome (aHUS)FASEB JOURNAL, 2008, 22Miller, Elizabeth C.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, St Louis, MO USA Washington Univ, Sch Med, St Louis, MO USALiszewski, M. Kathryn论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, St Louis, MO USA Washington Univ, Sch Med, St Louis, MO USAGupta, Ritu论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, St Louis, MO USA Washington Univ, Sch Med, St Louis, MO USAHauhart, Richard论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, St Louis, MO USA Washington Univ, Sch Med, St Louis, MO USAFremeaux-Bacchi, Veronique论文数: 0 引用数: 0 h-index: 0机构: Ctr Rech Biomed Cordeliers, Serv Immunol Biol, Paris, France Washington Univ, Sch Med, St Louis, MO USAGoodship, Timothy论文数: 0 引用数: 0 h-index: 0机构: Newcastle Univ, Inst Human Genet, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England Washington Univ, Sch Med, St Louis, MO USAAtkinson, John论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, St Louis, MO USA Washington Univ, Sch Med, St Louis, MO USA
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- [6] Mutations in complement factor I predispose to development of atypical hemolytic uremic syndromeJOURNAL OF THE AMERICAN SOCIETY OF NEPHROLOGY, 2005, 16 (07): : 2150 - 2155Kavanagh, D论文数: 0 引用数: 0 h-index: 0机构: Univ Newcastle Upon Tyne, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, EnglandKemp, EJ论文数: 0 引用数: 0 h-index: 0机构: Univ Newcastle Upon Tyne, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, EnglandMayland, E论文数: 0 引用数: 0 h-index: 0机构: Univ Newcastle Upon Tyne, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, EnglandWinney, RJ论文数: 0 引用数: 0 h-index: 0机构: Univ Newcastle Upon Tyne, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, EnglandDuffield, JS论文数: 0 引用数: 0 h-index: 0机构: Univ Newcastle Upon Tyne, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, EnglandWarwick, G论文数: 0 引用数: 0 h-index: 0机构: Univ Newcastle Upon Tyne, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, EnglandRichards, A论文数: 0 引用数: 0 h-index: 0机构: Univ Newcastle Upon Tyne, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, EnglandWard, R论文数: 0 引用数: 0 h-index: 0机构: Univ Newcastle Upon Tyne, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, EnglandGoodship, JA论文数: 0 引用数: 0 h-index: 0机构: Univ Newcastle Upon Tyne, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, EnglandGoodship, THJ论文数: 0 引用数: 0 h-index: 0机构: Univ Newcastle Upon Tyne, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England Univ Newcastle Upon Tyne, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England
- [7] Successful Treatment of Atypical Hemolytic Uremic Syndrome with the Complement Inhibitor EculizumabBLOOD, 2008, 112 (11) : 800 - 800Nuernberger, Jens论文数: 0 引用数: 0 h-index: 0机构: Univ Duisburg Essen, Dept Nephrol, Essen, Germany Univ Duisburg Essen, Dept Nephrol, Essen, GermanyWitzke, Oliver论文数: 0 引用数: 0 h-index: 0机构: Univ Duisburg Essen, Dept Nephrol, Essen, Germany Univ Duisburg Essen, Dept Nephrol, Essen, GermanyRother, Russell P.论文数: 0 引用数: 0 h-index: 0机构: Alex Pharmaceut, Cheshire, CT USA Univ Duisburg Essen, Dept Nephrol, Essen, GermanyPhilipp, Thomas论文数: 0 引用数: 0 h-index: 0机构: Univ Duisburg Essen, Dept Nephrol, Essen, Germany Univ Duisburg Essen, Dept Nephrol, Essen, GermanyVester, Udo论文数: 0 引用数: 0 h-index: 0机构: Univ Duisburg Essen, Dept Nephrol, Essen, Germany Univ Duisburg Essen, Dept Nephrol, Essen, GermanyBaba, Hideo论文数: 0 引用数: 0 h-index: 0机构: Univ Duisburg Essen, Dept Nephrol, Essen, Germany Univ Duisburg Essen, Dept Nephrol, Essen, GermanyZimmerhackl, Lothar Bemd论文数: 0 引用数: 0 h-index: 0机构: Innsbruck Med Univ, Dept Pediat, Innsbruck, Austria Univ Duisburg Essen, Dept Nephrol, Essen, Germany论文数: 引用数: h-index:机构:
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- [9] Mapping interactions between complement C3 and regulators using mutations in atypical hemolytic uremic syndromeBLOOD, 2015, 125 (15) : 2359 - 2369Schramm, Elizabeth C.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USARoumenina, Lubka T.论文数: 0 引用数: 0 h-index: 0机构: Cordeliers Res Ctr, INSERM, UMRS 1138, F-75006 Paris, France Univ Paris 05, Sorbonne Paris Cite, Paris, France Univ Paris 06, Paris, France Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USARybkine, Tania论文数: 0 引用数: 0 h-index: 0机构: Cordeliers Res Ctr, INSERM, UMRS 1138, F-75006 Paris, France Univ Paris 05, Sorbonne Paris Cite, Paris, France Univ Paris 06, Paris, France Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USAChauvet, Sophie论文数: 0 引用数: 0 h-index: 0机构: Cordeliers Res Ctr, INSERM, UMRS 1138, F-75006 Paris, France Univ Paris 05, Sorbonne Paris Cite, Paris, France Univ Paris 06, Paris, France Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USAVieira-Martins, Paula论文数: 0 引用数: 0 h-index: 0机构: Cordeliers Res Ctr, INSERM, UMRS 1138, F-75006 Paris, France Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USAHue, Christophe论文数: 0 引用数: 0 h-index: 0机构: Cordeliers Res Ctr, INSERM, UMRS 1138, F-75006 Paris, France Univ Paris 05, Sorbonne Paris Cite, Paris, France Univ Paris 06, Paris, France Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USAMaga, Tara论文数: 0 引用数: 0 h-index: 0机构: Univ Iowa, Mol Otolaryngol & Renal Res Labs, Iowa City, IA USA Univ Iowa, Dept Pediat, Carver Coll Med, Rare Renal Dis Clin, Iowa City, IA 52242 USA Univ Iowa, Dept Internal Med, Carver Coll Med, Rare Renal Dis Clin, Iowa City, IA 52242 USA Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USAValoti, Elisabetta论文数: 0 引用数: 0 h-index: 0机构: Mario Negri Inst Pharmacol Res, Lab Immunol & Genet Transplantat & Rare Dis, Ranica Bergamo, Italy Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USAWilson, Valerie论文数: 0 引用数: 0 h-index: 0机构: Newcastle upon Tyne Hosp NHS Fdn Trust, Northern Mol Genet Serv, Newcastle Upon Tyne, Tyne & Wear, England Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USAJokiranta, Sakari论文数: 0 引用数: 0 h-index: 0机构: Univ Helsinki, Dept Bacteriol & Immunol, Medicum, Helsinki, Finland Univ Helsinki, Res Programs Unit, Immunobiol, Helsinki, Finland Helsinki Univ Hosp, Helsinki, Finland Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USASmith, Richard J. H.论文数: 0 引用数: 0 h-index: 0机构: Univ Iowa, Mol Otolaryngol & Renal Res Labs, Iowa City, IA USA Univ Iowa, Dept Pediat, Carver Coll Med, Rare Renal Dis Clin, Iowa City, IA 52242 USA Univ Iowa, Dept Internal Med, Carver Coll Med, Rare Renal Dis Clin, Iowa City, IA 52242 USA Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USANoris, Marina论文数: 0 引用数: 0 h-index: 0机构: Mario Negri Inst Pharmacol Res, Lab Immunol & Genet Transplantat & Rare Dis, Ranica Bergamo, Italy Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USAGoodship, Tim论文数: 0 引用数: 0 h-index: 0机构: Newcastle Univ, Inst Med Genet, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USAAtkinson, John P.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USAFremeaux-Bacchi, Veronique论文数: 0 引用数: 0 h-index: 0机构: Cordeliers Res Ctr, INSERM, UMRS 1138, F-75006 Paris, France Univ Paris 05, Sorbonne Paris Cite, Paris, France Univ Paris 06, Paris, France Hop Europeen Georges Pompidou, Assistance Publ Hop Paris, Serv Immunol Biol, Paris, France Washington Univ, Sch Med, Dept Med, Div Rheumatol, St Louis, MO 63110 USA
- [10] Eculizumab treatment of atypical hemolytic uremic syndromeEXPERT OPINION ON ORPHAN DRUGS, 2013, 1 (02): : 167 - 176Kaplan, Bernard S.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Nephrol, Dept Pediat, Philadelphia, PA 19014 USA Childrens Hosp Philadelphia, Div Nephrol, Dept Pediat, Philadelphia, PA 19014 USARuebner, Rebecca L.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Nephrol, Dept Pediat, Philadelphia, PA 19014 USA Childrens Hosp Philadelphia, Div Nephrol, Dept Pediat, Philadelphia, PA 19014 USACopelovitch, Lawrence论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Nephrol, Dept Pediat, Philadelphia, PA 19014 USA Childrens Hosp Philadelphia, Div Nephrol, Dept Pediat, Philadelphia, PA 19014 USA