shRNA-Mediated Gene Therapy for the Treatment of Angelman Syndrome

被引：0
|
作者：
Kang, Hye Ri [1 ,2 ]
Zaric, Violeta [1 ]
Rahim, Aymun [1 ]
DeVries, Samantha P. [1 ]
Ma, Yuanqing [1 ]
Gumusgoz, Emrah [2 ]
Minassian, Berge [2 ]
Gray, Steven J. [2 ]
Butler, Ryan K. [1 ,2 ]
机构：
[1] UT Southwestern Med Ctr, Psychiat, Dallas, TX USA
[2] UT SouthWestern Med Ctr, Pediat, Dallas, TX USA
来源：
MOLECULAR THERAPY | 2022年 / 30卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
557
引用
收藏
页码：264 / 264
页数：1
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