CRISPR Genome Editing in Microphysiological Human Tissue System Models of Duchenne Muscular Dystrophy

被引:0
|
作者
Sitton, Madeleine J. [1 ]
Khodabukus, Alastair [1 ]
McCullough, K. Tyler [1 ]
Bursac, Nenad [1 ]
Gersbach, Charles A. [1 ]
机构
[1] Duke Univ, Biomed Engn, Durham, NC USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
1071
引用
收藏
页码:500 / 500
页数:1
相关论文
共 50 条
  • [1] Modeling Gene Editing Outcomes in Microphysiological Human Tissue System Models of Duchenne Muscular Dystrophy
    Sitton, Madeleine J.
    Khodabukus, Alastair
    Bohning, Joel D.
    Bursac, Nenad
    Gersbach, Charles A.
    [J]. MOLECULAR THERAPY, 2023, 31 (04) : 65 - 65
  • [2] Genome editing for Duchenne muscular dystrophy
    Gersbach, C. A.
    Nelson, C. E.
    Robinson-Hamm, J. N.
    [J]. HUMAN GENE THERAPY, 2016, 27 (11) : A20 - A20
  • [3] Genome editing for Duchenne muscular dystrophy
    Gersbach, C.
    Nelson, C.
    Robinson-Hamm, J.
    Kwon, J.
    Gough, V.
    Gemberling, M.
    [J]. NEUROMUSCULAR DISORDERS, 2018, 28 : S90 - S90
  • [4] Genome editing as a therapy for Duchenne muscular dystrophy
    Gersbach, Charles
    Nelson, Christopher
    Robinson-Hamm, Jacqueline
    Kwon, Jennifer
    [J]. ABSTRACTS OF PAPERS OF THE AMERICAN CHEMICAL SOCIETY, 2018, 256
  • [5] CRISPR-Editing Therapy for Duchenne Muscular Dystrophy
    Chemello, Francesco
    Olson, Eric N.
    Bassel-Duby, Rhonda
    [J]. HUMAN GENE THERAPY, 2023, 34 (9-10) : 379 - 387
  • [6] Delivery challenges for CRISPR-Cas9 genome editing for Duchenne muscular dystrophy
    Padmaswari, Made Harumi
    Agrawal, Shilpi
    Jia, Mary S.
    Ivy, Allie
    Maxenberger, Daniel A.
    Burcham, Landon A.
    Nelson, Christopher E.
    [J]. BIOPHYSICS REVIEWS, 2023, 4 (01):
  • [7] Genome editing for Duchenne muscular dystrophy: a glimpse of the future?
    Christian Kupatt
    Alina Windisch
    Alessandra Moretti
    Eckhard Wolf
    Wolfgang Wurst
    Maggie C. Walter
    [J]. Gene Therapy, 2021, 28 : 542 - 548
  • [8] Genome editing for Duchenne muscular dystrophy: a glimpse of the future?
    Kupatt, Christian
    Windisch, Alina
    Moretti, Alessandra
    Wolf, Eckhard
    Wurst, Wolfgang
    Walter, Maggie C.
    [J]. GENE THERAPY, 2021, 28 (09) : 542 - 548
  • [9] Long-Term Evaluation of AAV-CRISPR Genome Editing for Duchenne Muscular Dystrophy
    Nelson, Christopher
    Wu, Yaoying
    Gemberling, Matthew
    Oliver, Matthew
    Bohning, Joel D.
    Robinson-Hamm, Jacqueline N.
    Bulaklak, Karen
    Rivera, Ruth M. Castellanos
    Collier, Joel H.
    Asokan, Aravind
    Gersbach, Charles A.
    [J]. MOLECULAR THERAPY, 2019, 27 (04) : 46 - 47
  • [10] Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy
    Christopher E. Nelson
    Yaoying Wu
    Matthew P. Gemberling
    Matthew L. Oliver
    Matthew A. Waller
    Joel D. Bohning
    Jacqueline N. Robinson-Hamm
    Karen Bulaklak
    Ruth M. Castellanos Rivera
    Joel H. Collier
    Aravind Asokan
    Charles A. Gersbach
    [J]. Nature Medicine, 2019, 25 : 427 - 432