A real-world experience with long-term elapegademase treatment for adenosine deaminase deficiency

被引：0

作者：

Murguia-Favela, Luis ^{[1
]}

Suresh, Sneha ^{[2
]}

Wright, Nicola ^{[1
]}

Alvi, Saima ^{[3
]}

Tehseen, Sarah ^{[4
]}

Hernandez-Trujillo, Vivian ^{[5
]}

Seroogy, Christine ^{[6
]}

Nieves, Daime ^{[7
]}

Walter, Jolan ^{[8
,9
,10
]}

Keller, Michael ^{[11
]}

Pham-Huy, Anne ^{[12
]}

Grunebaum, Eyal ^{[13
]}

机构：

[1] Alberta Childrens Prov Gen Hosp, Calgary, AB, Canada

[2] Univ Alberta, Edmonton, AB, Canada

[3] Pediat Oncol Saskatchewan Canc Agcy, Regina, SK, Canada

[4] Jim Pattison Childrens Hosp, Saskatoon, SK, Canada

[5] Nicklaus Childrens Hosp, Miami, FL USA

[6] Univ Wisconsin, Madison, WI 53706 USA

[7] USF Hlth Allergy Immunol, Tampa, FL USA

[8] Univ S Florida, Morsani Coll Med, Tampa, FL 33620 USA

[9] Johns Hopkins All Childrens Hosp, St Petersburg, FL USA

[10] Massachusetts Gen Hosp Children, Boston, MA USA

[11] Childrens Natl Hosp, Washington, DC USA

[12] CHEO, Ottawa, ON, Canada

[13] Univ Toronto, Toronto, ON, Canada

来源：

JOURNAL OF CLINICAL IMMUNOLOGY | 2022年 / 42卷 / SUPPL 1期

关键词：

adenosine deaminase; SCID; Enzyme replacement; Long-term;

D O I：

暂无

中图分类号：

R392 [医学免疫学]; Q939.91 [免疫学];

学科分类号：

100102 ;

摘要：

引用

下载

页码：S24 / S24

页数：1

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