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- [1] Gene therapy cures the anemia and lethal bone marrow failure in a mouse model of RPS19-deficient Diamond-Blackfan anemiaHAEMATOLOGICA, 2014, 99 (12) : 1792 - 1798Jaako, Pekka论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Lund Strateg Ctr Stem Cell Biol, S-22100 Lund, Sweden Lund Univ, Lund Strateg Ctr Stem Cell Biol, S-22100 Lund, SwedenDebnath, Shubhranshu论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Lund Strateg Ctr Stem Cell Biol, S-22100 Lund, Sweden Lund Univ, Lund Strateg Ctr Stem Cell Biol, S-22100 Lund, SwedenOlsson, Karin论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Lund Strateg Ctr Stem Cell Biol, S-22100 Lund, Sweden Lund Univ, Lund Strateg Ctr Stem Cell Biol, S-22100 Lund, SwedenModlich, Ute论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Inst Expt Hematol, Hannover, Germany Paul Ehrlich Inst, LOEWE Res Grp Gene Modificat Stem Cells, D-63225 Langen, Germany Lund Univ, Lund Strateg Ctr Stem Cell Biol, S-22100 Lund, SwedenRothe, Michael论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Inst Expt Hematol, Hannover, Germany Lund Univ, Lund Strateg Ctr Stem Cell Biol, S-22100 Lund, SwedenSchambach, Axel论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Inst Expt Hematol, Hannover, Germany Lund Univ, Lund Strateg Ctr Stem Cell Biol, S-22100 Lund, SwedenFlygare, Johan论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Lund Strateg Ctr Stem Cell Biol, S-22100 Lund, Sweden Lund Univ, Lund Strateg Ctr Stem Cell Biol, S-22100 Lund, SwedenKarlsson, Stefan论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Lund Strateg Ctr Stem Cell Biol, S-22100 Lund, Sweden Lund Univ, Lund Strateg Ctr Stem Cell Biol, S-22100 Lund, Sweden
- [2] Preclinical studies for lentiviral-mediated gene therapy of RPS19-deficient Diamond-Blackfan anemiaHUMAN GENE THERAPY, 2021, 32 (19-20) : A83 - A84Gimenez, Y.论文数: 0 引用数: 0 h-index: 0机构: CIBERER, CIEMAT, Madrid, Spain IIS Fundac Jimenez Diaz, Madrid, Spain CIBERER, CIEMAT, Madrid, SpainPalacios, M.论文数: 0 引用数: 0 h-index: 0机构: CIBERER, CIEMAT, Madrid, Spain IIS Fundac Jimenez Diaz, Madrid, Spain CIBERER, CIEMAT, Madrid, SpainSanchez, R.论文数: 0 引用数: 0 h-index: 0机构: CIBERER, CIEMAT, Madrid, Spain IIS Fundac Jimenez Diaz, Madrid, Spain CIBERER, CIEMAT, Madrid, SpainZorbas, C.论文数: 0 引用数: 0 h-index: 0机构: ULB Canc Res Ctr, Brussels, Belgium CIBERER, CIEMAT, Madrid, SpainUgalde, L.论文数: 0 引用数: 0 h-index: 0机构: CIBERER, CIEMAT, Madrid, Spain IIS Fundac Jimenez Diaz, Madrid, Spain CIBERER, CIEMAT, Madrid, SpainAlberquilla, O.论文数: 0 引用数: 0 h-index: 0机构: CIBERER, CIEMAT, Madrid, Spain IIS Fundac Jimenez Diaz, Madrid, Spain CIBERER, CIEMAT, Madrid, SpainGalvez, E.论文数: 0 引用数: 0 h-index: 0机构: Hosp Nino Jesus, Madrid, Spain CIBERER, CIEMAT, Madrid, SpainStrullu, M.论文数: 0 引用数: 0 h-index: 0机构: Hop Robert Debre, Paris, France CIBERER, CIEMAT, Madrid, SpainSegovia, J. C.论文数: 0 引用数: 0 h-index: 0机构: CIBERER, CIEMAT, Madrid, Spain IIS Fundac Jimenez Diaz, Madrid, Spain CIBERER, CIEMAT, Madrid, SpainCatala, A.论文数: 0 引用数: 0 h-index: 0机构: Hosp San Juan Dios, Barcelona, Spain CIBERER, CIEMAT, Madrid, SpainRio, P.论文数: 0 引用数: 0 h-index: 0机构: CIBERER, CIEMAT, Madrid, Spain IIS Fundac Jimenez Diaz, Madrid, Spain CIBERER, CIEMAT, Madrid, SpainSevilla, J.论文数: 0 引用数: 0 h-index: 0机构: CIBERER, CIEMAT, Madrid, SpainBelendez, C.论文数: 0 引用数: 0 h-index: 0机构: Hosp Gregorio Maranon, Madrid, Spain CIBERER, CIEMAT, Madrid, SpainLafontaine, D. L. J.论文数: 0 引用数: 0 h-index: 0机构: ULB Canc Res Ctr, Brussels, Belgium CIBERER, CIEMAT, Madrid, SpainLeblanc, T.论文数: 0 引用数: 0 h-index: 0机构: Hop Robert Debre, Paris, France CIBERER, CIEMAT, Madrid, SpainBueren, J.论文数: 0 引用数: 0 h-index: 0机构: CIBERER, CIEMAT, Madrid, Spain IIS Fundac Jimenez Diaz, Madrid, Spain CIBERER, CIEMAT, Madrid, SpainNavarro, S.论文数: 0 引用数: 0 h-index: 0机构: CIBERER, CIEMAT, Madrid, Spain IIS Fundac Jimenez Diaz, Madrid, Spain CIBERER, CIEMAT, Madrid, Spain
- [3] Lentiviral-Mediated Preclinical Studies for the Gene Therapy of RPS19-Deficient Diamond-Blackfan Anemia PatientsMOLECULAR THERAPY, 2020, 28 (04) : 352 - 352Gimenez, Yari论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, Spain UAM, Fdn Jimenez Diaz, IIS, Adv Therapies Unit, Madrid, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainSanchez, Rebeca论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, Spain UAM, Fdn Jimenez Diaz, IIS, Adv Therapies Unit, Madrid, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainZorbas, Christiane论文数: 0 引用数: 0 h-index: 0机构: Univ Libre Bruxelles, ULB Canc Res Ctr, RNA Mol Biol, Brussels, Belgium CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainPalacios, Manuel论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, Spain UAM, Fdn Jimenez Diaz, IIS, Adv Therapies Unit, Madrid, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainUgalde, Laura论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, Spain UAM, Fdn Jimenez Diaz, IIS, Adv Therapies Unit, Madrid, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainAlberquilla, Omaira论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, Spain UAM, Fdn Jimenez Diaz, IIS, Adv Therapies Unit, Madrid, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainGalvez, Eva论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus, Madrid, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainStrullu, Marion论文数: 0 引用数: 0 h-index: 0机构: Hop Robert Debre, Serv Hematol Pediat, Paris, France CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainCarlos Segovia, Jose论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, Spain UAM, Fdn Jimenez Diaz, IIS, Adv Therapies Unit, Madrid, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainCatala, Albert论文数: 0 引用数: 0 h-index: 0机构: Hosp San Joan de Deu, Barcelona, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainRio, Paula论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, Spain UAM, Fdn Jimenez Diaz, IIS, Adv Therapies Unit, Madrid, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainSevilla, Julian论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus, Madrid, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainBelendez, Cristina论文数: 0 引用数: 0 h-index: 0机构: Hosp Gregorio Maranon, Madrid, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainLafontaine, Denis论文数: 0 引用数: 0 h-index: 0机构: Univ Libre Bruxelles, ULB Canc Res Ctr, RNA Mol Biol, Brussels, Belgium CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainLeblanc, Thierry论文数: 0 引用数: 0 h-index: 0机构: Hop Robert Debre, Serv Hematol Pediat, Paris, France CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainBueren, Juan论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, Spain UAM, Fdn Jimenez Diaz, IIS, Adv Therapies Unit, Madrid, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, SpainNavarro, Susana论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, Spain UAM, Fdn Jimenez Diaz, IIS, Adv Therapies Unit, Madrid, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, Madrid, Spain
- [4] Targeting RPS19 revisited: a new mouse model for Diamond-Blackfan AnemiaTRANSGENIC RESEARCH, 2016, 25 (02) : 262 - 262Schuster, Bjoern论文数: 0 引用数: 0 h-index: 0机构: ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech Republic ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech RepublicKanchev, Ivan论文数: 0 引用数: 0 h-index: 0机构: ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech Republic ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech RepublicChalupsky, Karel论文数: 0 引用数: 0 h-index: 0机构: ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech Republic ASCR, Inst Mol Genet, Dept Transgen Models Dis, Prague, Czech Republic ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech RepublicRuberte, Jesus论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Sch Vet Med, Dept Anat & Anim Hlth, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Barcelona, Spain ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech RepublicProchazka, Jan论文数: 0 引用数: 0 h-index: 0机构: ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech Republic ASCR, Inst Mol Genet, Dept Transgen Models Dis, Prague, Czech Republic ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech RepublicMaceckova, Zuzana论文数: 0 引用数: 0 h-index: 0机构: Palacky Univ, Fac Med & Dent, CR-77147 Olomouc, Czech Republic Univ Hosp, Olomouc, Czech Republic ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech RepublicPospisilova, Dagmar论文数: 0 引用数: 0 h-index: 0机构: Palacky Univ, Fac Med & Dent, CR-77147 Olomouc, Czech Republic Univ Hosp, Olomouc, Czech Republic ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech RepublicHajduch, Marian论文数: 0 引用数: 0 h-index: 0机构: Palacky Univ, Fac Med & Dent, CR-77147 Olomouc, Czech Republic Univ Hosp, Olomouc, Czech Republic ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech RepublicReinis, Milan论文数: 0 引用数: 0 h-index: 0机构: ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech Republic ASCR, Inst Mol Genet, Dept Transgen Models Dis, Prague, Czech Republic ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech RepublicLastuvkova, Anna论文数: 0 引用数: 0 h-index: 0机构: ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech Republic ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech RepublicPalesova, Henrieta论文数: 0 引用数: 0 h-index: 0机构: ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech Republic ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech RepublicSpoutil, Frantisek论文数: 0 引用数: 0 h-index: 0机构: ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech Republic ASCR, Inst Mol Genet, Dept Transgen Models Dis, Prague, Czech Republic ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech RepublicKopkanova, Jana论文数: 0 引用数: 0 h-index: 0机构: ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech Republic ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech RepublicBeck, Inken M.论文数: 0 引用数: 0 h-index: 0机构: ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech Republic ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech RepublicSedlacek, Radislav论文数: 0 引用数: 0 h-index: 0机构: ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech Republic ASCR, Inst Mol Genet, Dept Transgen Models Dis, Prague, Czech Republic ASCR, Inst Mol Genet, Czech Ctr Phenogen, Prague, Czech Republic
- [5] Disturbed ribosome biogenesis, cell cycle arrest and increased apoptosis in RPS19-deficient erythroid progenitors provide clues to Diamond-Blackfan anemia pathogenesisEXPERIMENTAL HEMATOLOGY, 2007, 35 (09) : 11 - 11论文数: 引用数: h-index:机构:
- [6] Preclinical Gene Therapy in Hematopoietic Stem and Progenitor Cells from RPS19-Deficient Diamond-Blackfan Anemia PatientsMOLECULAR THERAPY, 2021, 29 (04) : 335 - 336Gimenez, Yari论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSanchez, Rebeca论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainZorbas, Christiane论文数: 0 引用数: 0 h-index: 0机构: Univ Libre Bruxelles, ULB Canc Res Ctr U CRC, 3RNA Mol Biol, Bruxeles, Belgium Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainPalacios, Manuel论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainUgalde, Laura论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainAlberquilla, Omaira论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainGalvez, Eva论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Hosp Infantil Univ Nino Jesus, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainStrullu, Marion论文数: 0 引用数: 0 h-index: 0机构: Hop Robert Debre, Paris, France Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSegovia, Jose C.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainCatala, Albert论文数: 0 引用数: 0 h-index: 0机构: Hosp St Joan de Deu, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainRio, Paula论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSevilla, Julian论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainBelendez, Cristina论文数: 0 引用数: 0 h-index: 0机构: Hosp Gregorio Maranon, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainLafontaine, Denis论文数: 0 引用数: 0 h-index: 0机构: Univ Libre Bruxelles, ULB Canc Res Ctr U CRC, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainLeblanc, Thierry论文数: 0 引用数: 0 h-index: 0机构: Hop Robert Debre, Paris, France Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainBueren, Juan论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainNavarro, Susana论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain
- [7] ENFORCED EXPRESSION OF RPS19 DERIVED FROM HUMAN ELONGATION FACTOR 1A SHORT (EFS) PROMOTER CORRECTS THE ANEMIA AND LETHAL BONE MARROW FAILURE IN MOUSE MODEL FOR RPS19-DEFICIENT DIAMOND-BLACKFAN ANEMIAEXPERIMENTAL HEMATOLOGY, 2015, 43 (09) : S59 - S59Debnath, Shubhranshu论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Lund, Skane, Sweden Lund Univ, Lund, Skane, SwedenJaako, Pekka论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Lund, Skane, Sweden Lund Univ, Lund, Skane, SwedenSiva, Kavitha论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Lund, Skane, Sweden Lund Univ, Lund, Skane, SwedenModlich, Ute论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst Fed Inst Vaccines & Biomed, Langen, Germany Hannover Med Sch, Inst Expt Hematol, Hannover, Germany Lund Univ, Lund, Skane, SwedenSchambach, Axel论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Inst Expt Hematol, Hannover, Germany Lund Univ, Lund, Skane, SwedenGaspar, Bobby论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Child Hlth, Mol Immunol Unit, London, England Lund Univ, Lund, Skane, Sweden论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:
- [8] Single-Cell-Multiomics Demonstrates Molecular Efficacy of a Clinical Lentiviral Vector for Gene Therapy of RPS19-Deficient Diamond-Blackfan AnemiaBLOOD, 2023, 142Freiman, Sofia论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Lund Stem Cell Ctr, Lund, Sweden Lund Univ, Lund Stem Cell Ctr, Lund, SwedenChen, Jun论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Lund Stem Cell Ctr, Lund, Sweden Lund Univ, Lund Stem Cell Ctr, Lund, SwedenFlygare, Johan论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Lund Stem Cell Ctr, Lund, Sweden Lund Univ, Lund Stem Cell Ctr, Lund, SwedenKampman, Chayenne论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Med Ctr, Leiden, Netherlands Lund Univ, Lund Stem Cell Ctr, Lund, SwedenPike-Overzet, Karin论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Med Ctr, Leiden, Netherlands Lund Univ, Lund Stem Cell Ctr, Lund, SwedenMohseny, Alexander论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Med Ctr, Leiden, Netherlands Lund Univ, Lund Stem Cell Ctr, Lund, SwedenHa, Teng-Cheong论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Inst Expt Hematol, Hannover, Germany Lund Univ, Lund Stem Cell Ctr, Lund, SwedenLidgren, Mathias论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Lund Stem Cell Ctr, Lund, Sweden Lund Univ, Lund Stem Cell Ctr, Lund, SwedenSoneji, Shamit论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Lund Stem Cell Ctr, Lund, Sweden Lund Univ, Lund Stem Cell Ctr, Lund, Sweden论文数: 引用数: h-index:机构:Pospisilova, Dagmar论文数: 0 引用数: 0 h-index: 0机构: Palacky Univ, Dept Pediat, Olomouc, Czech Republic Univ Hosp, Olomouc, Czech Republic Lund Univ, Lund Stem Cell Ctr, Lund, SwedenStaal, Frank论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Med Ctr, Leiden, Netherlands Lund Univ, Lund Stem Cell Ctr, Lund, SwedenSchambach, Axel论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Inst Expt Hematol, Hannover, Germany Lund Univ, Lund Stem Cell Ctr, Lund, SwedenFlygare, Johan论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Lund Stem Cell Ctr, Lund, Sweden Lund Univ, Lund Stem Cell Ctr, Lund, Sweden
- [9] Defects of protein production in erythroid cells revealed in a zebrafish Diamond-Blackfan anemia model for mutation in RPS19CELL DEATH & DISEASE, 2014, 5 : e1352 - e1352Zhang, Y.论文数: 0 引用数: 0 h-index: 0机构: Peking Univ, Coll Life Sci, Minist Educ, Key Lab Cell Proliferat & Differentiat, Beijing 100871, Peoples R China Univ Calif Los Angeles, Dept Mol Cell & Dev Biol, Los Angeles, CA 90095 USA Peking Univ, Coll Life Sci, Minist Educ, Key Lab Cell Proliferat & Differentiat, Beijing 100871, Peoples R ChinaEar, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Mol Cell & Dev Biol, Los Angeles, CA 90095 USA Peking Univ, Coll Life Sci, Minist Educ, Key Lab Cell Proliferat & Differentiat, Beijing 100871, Peoples R ChinaYang, Z.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Mol Cell & Dev Biol, Los Angeles, CA 90095 USA Peking Univ, Coll Life Sci, Minist Educ, Key Lab Cell Proliferat & Differentiat, Beijing 100871, Peoples R ChinaMorimoto, K.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Mol Cell & Dev Biol, Los Angeles, CA 90095 USA Peking Univ, Coll Life Sci, Minist Educ, Key Lab Cell Proliferat & Differentiat, Beijing 100871, Peoples R ChinaZhang, B.论文数: 0 引用数: 0 h-index: 0机构: Peking Univ, Coll Life Sci, Minist Educ, Key Lab Cell Proliferat & Differentiat, Beijing 100871, Peoples R China Peking Univ, Coll Life Sci, Minist Educ, Key Lab Cell Proliferat & Differentiat, Beijing 100871, Peoples R ChinaLin, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Mol Cell & Dev Biol, Los Angeles, CA 90095 USA Peking Univ, Coll Life Sci, Minist Educ, Key Lab Cell Proliferat & Differentiat, Beijing 100871, Peoples R China
- [10] Diamond-Blackfan anemia with mutations in RPS19 gene:: A different pattern of in vitro erythroid differentiation?BLOOD, 1999, 94 (10) : 414A - 414ACroisille, L论文数: 0 引用数: 0 h-index: 0机构: Hop Kremlin Bicetre, Dept Hematol, Paris, FranceChiron, M论文数: 0 引用数: 0 h-index: 0机构: Hop Kremlin Bicetre, Dept Hematol, Paris, FranceVainchenker, W论文数: 0 引用数: 0 h-index: 0机构: Hop Kremlin Bicetre, Dept Hematol, Paris, FranceRomeo, PH论文数: 0 引用数: 0 h-index: 0机构: Hop Kremlin Bicetre, Dept Hematol, Paris, FranceRince, P论文数: 0 引用数: 0 h-index: 0机构: Hop Kremlin Bicetre, Dept Hematol, Paris, FranceWillig, TN论文数: 0 引用数: 0 h-index: 0机构: Hop Kremlin Bicetre, Dept Hematol, Paris, FranceTchernia, G论文数: 0 引用数: 0 h-index: 0机构: Hop Kremlin Bicetre, Dept Hematol, Paris, France