Preclinical studies of hematopoietic stem cell gene therapy in the mouse model of types A and B Niemann-Pick disease.

被引:0
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作者
Miranda, SRP [1 ]
Schuchman, EH [1 ]
机构
[1] Mt Sinai Sch Med, Dept Human Genet, New York, NY USA
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Q3 [遗传学];
学科分类号
071007 ; 090102 ;
摘要
2420
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页码:429 / 429
页数:1
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