Initiation of Oral Steroid Therapy Produced Rapid Normalization of Transaminase Levels and Stabilization of FIX Activity in Subjects Who Developed T-Cell Responses in the SPK-9001: AAV Gene Transfer for Hemophilia B Phase 1/2 Trial

被引:0
|
作者
George, L. [1 ]
Sullivan, S. [2 ]
Giermasz, A. [3 ]
Ducore, J. [4 ]
Rasko, J. [5 ]
Teitel, J. [6 ]
Cuker, A. [7 ]
Samelson-Jones, B. [1 ]
Sullivan, L. [8 ]
Majumdar, S. [8 ]
Mcguinn, C. [9 ]
Galvao, A. [1 ]
机构
[1] Childrens Hosp Philadelphia, Philadelphia, PA USA
[2] Mississippi Ctr Adv Med, Madison, MS USA
[3] UC Davis Canc Ctr, Sacramento, CA USA
[4] UC Davis Sch Med, Sacramento, CA USA
[5] Royal Prince Alfred Hosp, Sydney, NSW, Australia
[6] St Michaels Hosp, Hemophilia Treatment Ctr, Toronto, ON, Canada
[7] Univ Penn, Philadelphia, PA 19104 USA
[8] Univ Mississippi, Med Ctr, Jackson, MS 39216 USA
[9] Weill Cornell Med Ctr, New York, NY USA
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中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
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页码:15 / 16
页数:2
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