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- [1] Novel AAV Capsids for Intravitreal Delivery: Identifying and Characterizing Novel AAV Variants in Non-Human PrimatesMOLECULAR THERAPY, 2022, 30 (04) : 557 - 557Guerin, Karen论文数: 0 引用数: 0 h-index: 0机构: Vedere Bio II, R&D, Cambridge, MA USA Vedere Bio II, R&D, Cambridge, MA USAGeller, Scott论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Berkeley, Mol & Cell Biol, Berkeley, CA 94720 USA Vedere Bio II, R&D, Cambridge, MA USAFlannery, John G.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Berkeley, Mol & Cell Biol, Berkeley, CA 94720 USA Vedere Bio II, R&D, Cambridge, MA USAIsacoff, Ehud论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Berkeley, Mol & Cell Biol, Berkeley, CA 94720 USA Vedere Bio II, R&D, Cambridge, MA USABeltran, William A.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Div Expt Retinal Therapies, Philadelphia, PA 19104 USA Vedere Bio II, R&D, Cambridge, MA USAByrne, Leah C.论文数: 0 引用数: 0 h-index: 0机构: Univ Pittsburgh, Ophthalmol, Philadelphia, PA USA Vedere Bio II, R&D, Cambridge, MA USAOzturk, Bilge E.论文数: 0 引用数: 0 h-index: 0机构: Univ Pittsburgh, Ophthalmol, Philadelphia, PA USA Vedere Bio II, R&D, Cambridge, MA USAMozayeni, Cyrus论文数: 0 引用数: 0 h-index: 0机构: Vedere Bio II, R&D, Cambridge, MA USA Vedere Bio II, R&D, Cambridge, MA USA
- [2] Comparison of CNS Transduction by Different AAV Capsids in Mouse and Non-Human PrimateMOLECULAR THERAPY, 2015, 23 : S37 - S37Goulet, Martin论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USAAubin, Justin论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USAKells, Adrian P.论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USASu, Qin论文数: 0 引用数: 0 h-index: 0机构: UMMS, Gene Therapy Ctr, Worcester, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USAYuan, Shipeng论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USARamamoorthi, Kartik论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USAKotin, Rob论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USAMcLaughlin, James论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USAGao, Guangping论文数: 0 引用数: 0 h-index: 0机构: UMMS, Gene Therapy Ctr, Worcester, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USASah, Dinah W. Y.论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USA
- [3] NAVIGATE: A Directed Evolution Platform for Engineering Novel Ocular and Muscle AAV Capsids in Non-Human PrimatesMOLECULAR THERAPY, 2024, 32 (04) : 266 - 267Firnberg, Elad论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USATejada, Sigmund K. S.论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAYost, Samantha论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAGiles, April R.论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAGaynutdinov, Timur论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAChen, Victor论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAFoltz, Steven论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAElliot, Kirk论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAHeithoff, Benjamin P.论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USASmith, Jared B.论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAGumerson, Jessica论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USALilley, Brendan论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAKarumuthil-Melethil, Subha论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAChoi, Heonhwa论文数: 0 引用数: 0 h-index: 0机构: Rutgers State Univ, Inst Quantitat Biomed, Piscataway, NJ USA REGENXBIO Inc, Rockville, MD USAKaelber, Jason T.论文数: 0 引用数: 0 h-index: 0机构: Rutgers State Univ, Inst Quantitat Biomed, Piscataway, NJ USA REGENXBIO Inc, Rockville, MD USADanos, Olivier F.论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAMercer, Andrew C.论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USALiu, Ye论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USA
- [4] Comparative analysis of tropism of a large pool of AAV capsids in cell culture, mice, and non-human primatesHUMAN GENE THERAPY, 2022, 33 (23-24) : A31 - A31Mercer, A. C.论文数: 0 引用数: 0 h-index: 0机构: ReGenX Biosci, Rockville, MD USA ReGenX Biosci, Rockville, MD USAGiles, A. R.论文数: 0 引用数: 0 h-index: 0机构: ReGenX Biosci, Rockville, MD USA ReGenX Biosci, Rockville, MD USAYost, S. A.论文数: 0 引用数: 0 h-index: 0机构: ReGenX Biosci, Rockville, MD USA ReGenX Biosci, Rockville, MD USAFirnberg, E.论文数: 0 引用数: 0 h-index: 0机构: ReGenX Biosci, Rockville, MD USA ReGenX Biosci, Rockville, MD USACho, S.论文数: 0 引用数: 0 h-index: 0机构: ReGenX Biosci, Rockville, MD USA ReGenX Biosci, Rockville, MD USATejada, S.论文数: 0 引用数: 0 h-index: 0机构: ReGenX Biosci, Rockville, MD USA ReGenX Biosci, Rockville, MD USAEgley, J.论文数: 0 引用数: 0 h-index: 0机构: ReGenX Biosci, Rockville, MD USA ReGenX Biosci, Rockville, MD USASmith, J.论文数: 0 引用数: 0 h-index: 0机构: ReGenX Biosci, Rockville, MD USA ReGenX Biosci, Rockville, MD USAJanczura, K.论文数: 0 引用数: 0 h-index: 0机构: ReGenX Biosci, Rockville, MD USA ReGenX Biosci, Rockville, MD USAKarumuthil-Melethil, S.论文数: 0 引用数: 0 h-index: 0机构: ReGenX Biosci, Rockville, MD USA ReGenX Biosci, Rockville, MD USADanos, O.论文数: 0 引用数: 0 h-index: 0机构: ReGenX Biosci, Rockville, MD USA ReGenX Biosci, Rockville, MD USALiu, Y.论文数: 0 引用数: 0 h-index: 0机构: ReGenX Biosci, Rockville, MD USA ReGenX Biosci, Rockville, MD USA
- [5] Novel AAV Capsids Demonstrate Strong Retinal Expression in Non-Human Primates After Intravitreal AdministrationINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2019, 60 (09)Kevany, Brian论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut LLC, Prod Dev, Cleveland, OH USA Abeona Therapeut LLC, Prod Dev, Cleveland, OH USASuh, Susie论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Ophthalmol, Irvine, CA USA Abeona Therapeut LLC, Prod Dev, Cleveland, OH USALu, Jennings论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Ophthalmol, Irvine, CA USA Abeona Therapeut LLC, Prod Dev, Cleveland, OH USAPadegimas, Linas论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut LLC, Prod Dev, Cleveland, OH USA Abeona Therapeut LLC, Prod Dev, Cleveland, OH USAPalczewski, Krzysztof论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Ophthalmol, Irvine, CA USA Abeona Therapeut LLC, Prod Dev, Cleveland, OH USAMiller, Timothy论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut LLC, Prod Dev, Cleveland, OH USA Abeona Therapeut LLC, Prod Dev, Cleveland, OH USA
- [6] Novel AAV Capsids Demonstrate Strong Retinal Expression in Non-Human Primates after Intravitreal AdministrationMOLECULAR THERAPY, 2019, 27 (04) : 113 - 113Kevany, Brian M.论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut Inc, Cleveland, OH USA Abeona Therapeut Inc, Cleveland, OH USASuh, Susie论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Ophthalmol, Irvine, CA USA Univ Calif Irvine, Gavin Herbert Eye Inst, Irvine, CA USA Abeona Therapeut Inc, Cleveland, OH USALu, Jennings论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Irvine, CA USA Abeona Therapeut Inc, Cleveland, OH USAPadegimas, Linas论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut Inc, Cleveland, OH USA Abeona Therapeut Inc, Cleveland, OH USAPalczewski, Krzysztof论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Irvine, CA USA Abeona Therapeut Inc, Cleveland, OH USAMiller, Timothy J.论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut Inc, Cleveland, OH USA Abeona Therapeut Inc, Cleveland, OH USA
- [7] In vivo selection in non-human primates identifies AAV capsids for on-target CSF delivery to spinal cordMOLECULAR THERAPY, 2024, 32 (08) : 2584 - 2603Hanlon, Killian S.论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA UCL, London, England Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USACheng, Ming论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAFerrer, Roberto Montoro论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Dept Pediat Neurol, Amsterdam Neurosci, Emma Childrens Hospitaln,Amsterdam UMC,Amsterdam L, Amsterdam, Netherlands Vrije Univ Amsterdam, Ctr Neurogenom & Cognit Res, Dept Complex Trait Genet, Amsterdam Neurosci, Amsterdam, Netherlands Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USARyu, Jae Ryun论文数: 0 引用数: 0 h-index: 0机构: Korea Univ, Dept Anat, Brain Korea 21 Plus Program Biomed Sci, Coll Med, Seoul, South Korea Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USALee, Boram论文数: 0 引用数: 0 h-index: 0机构: Korea Univ, Dept Anat, Brain Korea 21 Plus Program Biomed Sci, Coll Med, Seoul, South Korea Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAde la Cruz, Demitri论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAPatel, Nikita论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAEspinoza, Paula论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USASantoscoy, Miguel C.论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAGong, Yi论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USANg, Carrie论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USANguyen, Diane M.论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USANammour, Josette论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAClark, Sean W.论文数: 0 引用数: 0 h-index: 0机构: SwanBio Therapeut, Bala Cynwyd 19005, PA USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAHeine, Vivi M.论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC, Emma Childrens Hosp, Dept Child & Adolescent Psychiat, Emma Ctr Personalized Med,Amsterdam Neurosci, Amsterdam, Netherlands Vrije Univ Amsterdam, Ctr Neurogen & Cognit Res, Dept Complex Trait Genet, Amsterdam Neurosci, Amsterdam, Netherlands Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USASun, Woong论文数: 0 引用数: 0 h-index: 0机构: Korea Univ, Dept Anat, Brain Korea 21 Plus Program Biomed Sci, Coll Med, Seoul, South Korea Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAKozarsky, Karen论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAMaguire, Casey A.论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA SwanBio Therapeut, Bala Cynwyd 19005, PA USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA
- [8] A Promising New Family of Peptide-Modified AAV Capsids for Gene Delivery to the Central Nervous System in Non-Human PrimatesMOLECULAR THERAPY, 2022, 30 (04) : 556 - 556Chan, Ken Y.论文数: 0 引用数: 0 h-index: 0机构: Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USA Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USAPacouret, Simon论文数: 0 引用数: 0 h-index: 0机构: Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USA Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USAHuang, Qin论文数: 0 引用数: 0 h-index: 0机构: Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USA Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USAZheng, Qingxia论文数: 0 引用数: 0 h-index: 0机构: Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USA Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USAVandenburg, Charles论文数: 0 引用数: 0 h-index: 0机构: Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USA Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USAWu, Jason论文数: 0 引用数: 0 h-index: 0机构: Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USA Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USABrauer, Pamela论文数: 0 引用数: 0 h-index: 0机构: Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USA Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USAZhang, Qiangge论文数: 0 引用数: 0 h-index: 0机构: MIT, McGovern Inst Brain Res, Cambridge, MA USA Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USATobey, Isabelle论文数: 0 引用数: 0 h-index: 0机构: Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USA Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USAWu, Carolyn论文数: 0 引用数: 0 h-index: 0机构: MIT, McGovern Inst Brain Res, Cambridge, MA USA Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USAChen, Albert T.论文数: 0 引用数: 0 h-index: 0机构: Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USA Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USAKozareva, Velina论文数: 0 引用数: 0 h-index: 0机构: Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USA Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USAFeng, Guoping论文数: 0 引用数: 0 h-index: 0机构: Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USA MIT, McGovern Inst Brain Res, Cambridge, MA USA Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USADeverman, Benjamin E.论文数: 0 引用数: 0 h-index: 0机构: Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USA Broad Inst MIT & Harvard, Stanley Ctr Psychiat Res, Cambridge, MA 02142 USA
- [9] Manufacturability and Product Quality of Novel AAV Capsids Optimized for Specific Targeting Using Capsid Library Selection in Non-Human PrimatesMOLECULAR THERAPY, 2022, 30 (04) : 534 - 534Acharya, Hari论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USAChu, David论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USACockrell, Adam论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USAGranados, Jesse论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USALiu, Carol论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USAMitchell, Alex论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USAMorales, Heidy论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USAPedeferri, Carrie论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USARodden, Jenna论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USASandberg, Troy论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USASimington, Claire论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USASpringfield, Emily论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USAWheeler, Brandon论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USAWheeler, Jordyn论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USAGoeden, Nick论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USAAdamson, Laura论文数: 0 引用数: 0 h-index: 0机构: Capsida Biotherapeut, Thousand Oaks, CA USA Capsida Biotherapeut, Thousand Oaks, CA USA
- [10] Immune-driven gene expression loss following intramuscular AAV delivery to non-human primates is only transientMOLECULAR THERAPY METHODS & CLINICAL DEVELOPMENT, 2025, 33 (01)Journou, Malo论文数: 0 引用数: 0 h-index: 0机构: Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, France Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, FranceDevaux, Marie论文数: 0 引用数: 0 h-index: 0机构: Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, France Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, FranceJaulin, Nicolas论文数: 0 引用数: 0 h-index: 0机构: Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, France Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, FrancePichard, Virginie论文数: 0 引用数: 0 h-index: 0机构: Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, France Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, FranceSegovia, Mercedes论文数: 0 引用数: 0 h-index: 0机构: Nantes Univ, CHU Nantes, ITUN Inst Transplantat Urol Nephrol, Ctr Rech Transplantat & Immunol,INSERM,UMR 1064, F-44200 Nantes, France Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, FranceMoreau, Aurelie论文数: 0 引用数: 0 h-index: 0机构: Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, France Nantes Univ, CHU Nantes, ITUN Inst Transplantat Urol Nephrol, Ctr Rech Transplantat & Immunol,INSERM,UMR 1064, F-44200 Nantes, France Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, FranceLe Duff, Johanne论文数: 0 引用数: 0 h-index: 0机构: Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, France Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, FranceCuturi, Maria Cristina论文数: 0 引用数: 0 h-index: 0机构: Nantes Univ, CHU Nantes, ITUN Inst Transplantat Urol Nephrol, Ctr Rech Transplantat & Immunol,INSERM,UMR 1064, F-44200 Nantes, France Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, FranceGuilbaud, Mickael论文数: 0 引用数: 0 h-index: 0机构: Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, France Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, FranceAdjali, Oumeya论文数: 0 引用数: 0 h-index: 0机构: Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, France Univ Nantes, CHU Nantes, INSERM UMR 1089, Translat Gene Therapy Genet Dis, F-44200 Nantes, France