[1] Newcastle Univ, Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, England
[2] Childrens Natl Hlth Syst, Div Biostat & Study Methodol, Ctr Translat Sci, Washington, DC USA
[3] George Washington Univ, Pediat Epidemiol & Biostat, Washington, DC USA
[4] Expt & Clin Res Ctr, Charite Muscle Res Unit, Berlin, Germany
[5] Stanford Univ, Sch Med, Dept Neurol & Neurol Sci, Stanford, CA 94305 USA
[6] Childrens Hosp Westmead, Inst Neurosci & Muscle Res, Sydney, NSW, Australia
[7] Childrens Natl Hlth Syst, Dept Neurol, Washington, DC USA
[8] Aix Marseille Univ, La Timone Hosp, Neuromuscular & ALS Ctr, Marseille, France
[9] Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA
[10] Ludwig Maximilians Univ Munchen, Dept Neurol, Friedrich Baur Inst, Munich, Germany
[11] Hosp Univ Virgen del Rocio, Inst Biomed Sevilla, Neuromuscular Unit, Dept Neurol, Seville, Spain
[12] GH Pitie Salpetriere, AP HP, Inst Myol, 47-83 Blvd Hop, Paris, France
[13] Natl Ctr Hosp, Natl Ctr Neurol & Psychiat, Dept Neurol, Tokyo, Japan
[14] Carolinas Healthcare Syst Neurosci Inst, Charlotte, NC USA
[15] Hosp Santa Creu & Sant Pau, Neuromuscular Disorders Unit, Neurol Dept, Barcelona, Spain
[16] Univ Padua, Dept Neurosci, Padua, Italy
[17] Nationwide Childrens Hosp, Columbus, OH USA