Autologous Ex Vivo Lentiviral Gene Therapy for the Treatment of ADA-SCID

被引：0

作者：

Booth, Claire ^{[1
]}

Kohn, Don B. ^{[2
]}

Shaw, Kit L. ^{[2
]}

Xu-Bayford, Jinhua ^{[3
]}

Garabedian, Elizabeth ^{[4
]}

Trevisan, Valentina ^{[1
]}

Carbonaro-Sarracino, Denise A. ^{[5
]}

Soni, Kajal ^{[1
]}

Terrazas, Dayna ^{[2
]}

Snell, Katie ^{[5
]}

Leon-Rico, Diego ^{[1
]}

Buckland, Karen ^{[1
]}

Gilmour, Kimberly ^{[1
]}

De Oliveira, Satiro ^{[2
]}

Rivat, Christine ^{[5
]}

Izotova, Natalia ^{[1
]}

Adams, Stuart ^{[1
]}

Ricketts, Hilory ^{[1
]}

Davila, Alejandra ^{[2
]}

Uzowuru, Chilenwa ^{[1
]}

Fernandez, Beatriz Campo ^{[2
]}

Hollis, Roger P. ^{[2
]}

Coronel, Maritess ^{[2
]}

Zhang, Ruixue ^{[2
]}

Arduini, Serena ^{[5
]}

Lynn, Frances ^{[5
]}

Kudari, Mahesh ^{[5
]}

Spezzi, Andrea ^{[5
]}

Zhan, Marco ^{[6
]}

Heimke, Rene ^{[6
]}

Labik, Ivan ^{[6
]}

Cornetta, Kenneth ^{[7
]}

Sokolic, Robert ^{[4
]}

Hershfield, Michael ^{[8
]}

Schmidt, Manfred ^{[6
]}

Candotti, Fabio ^{[9
]}

Malech, Harry L. ^{[10
]}

Thrasher, Adrian J. ^{[1
]}

Gaspar, H. Bobby ^{[5
]}

机构：

[1] UCL GOSH Inst Child Hlth, London, England

[2] Univ Calif Los Angeles, Los Angeles, CA USA

[3] Great Ormond St Hosp NHS Trust, London, England

[4] NHGRI, Bethesda, MD 20892 USA

[5] Orchard Therapeut, London, England

[6] GeneWerk, Heidelberg, Germany

[7] Indiana Univ Sch Med, Indianapolis, IN 46202 USA

[8] Duke Univ, Durham, NC USA

[9] Lausanne Univ Hosp, Lausanne, Switzerland

[10] NIAID, 9000 Rockville Pike, Bethesda, MD 20892 USA

来源：

MOLECULAR THERAPY | 2021年 / 29卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

引用

页码：20 / 20

页数：1

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