Safety and efficacy of a 22-week treatment with sapropterin dihydrochloride (tetrahydrobiopterin or 6R-BH4) in phenylketonuria (PKU)

被引：0
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作者：
Feillet, F.
Clarcke, L.
Lee, P.
Bebchuck, J.
Meli, C.
Bergoffen, J.
Dorenbaum, A.
Giovannini, M.
机构：
[1] CHU Brabois, Hop Enfants, Vandoeuvre Les Nancy, France
[2] UBC, Vancouver, BC, Canada
[3] UCL Natl Hosp Neurol, London, England
[4] Stat Collab Inc, Washington, DC USA
[5] Azienda Osped Univ, Catania, Italy
[6] So Calif Permanente Med Grp, Dept Genet, San Jose, CA USA
[7] Univ Milan, S Paolo Hosp, Dept Pediat, I-20122 Milan, Italy
来源：
JOURNAL OF INHERITED METABOLIC DISEASE | 2007年 / 30卷
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中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
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页码：17 / 17
页数：1
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