AAV Gene Therapy for Treating MPS IIIC: Facilitate by-Stander Effects by EV-mRNA Cargo

被引：0
|
作者：
Bobo, Tierra A. [1 ]
Robinson, Michael [2 ]
Sokolski-Papkov, Marina [3 ]
Fu, Haiyan [1 ]
机构：
[1] Univ N Carolina, Div Genet & Metab, Dept Pediat, Gene Therapy Ctr, Chapel Hill, NC USA
[2] Univ N Carolina, Gene Therapy, Chapel Hill, NC USA
[3] Univ N Carolina, Ctr Nanotechnol Drug Delivery, Chapel Hill, NC USA
来源：
MOLECULAR THERAPY | 2022年 / 30卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
248
引用
收藏
页码：120 / 121
页数：2
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