Safety Evaluation of IV-Administered BBP-812, an AAV9-Based Gene Therapy for the Treatment of Canavan Disease, in Mice and Juvenile Cynomolgus Macaques

被引：0

|

作者：

Scott, David W. ^{[1
]}

Rouse, Jeremy ^{[1
]}

Romero, Kirsten ^{[1
]}

Eclov, Rachel ^{[1
]}

Kapadia, Mayank ^{[1
]}

McCoy, Daniel ^{[1
]}

Beard, Clayton W. ^{[1
]}

机构：

[1] Aspa Therapeut, Raleigh, NC USA

来源：

MOLECULAR THERAPY | 2021年 / 29卷 / 04期

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D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

164

引用

收藏

页码：85 / 85

页数：1

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