Dual-Regulated Lentiviral Vector for Gene Therapy of X-linked Chronic Granulomatous Disease

被引：0

作者：

Farinelli, G. ^{[1
]}

Chiriaco, M. ^{[2
,3
]}

Capo, V. ^{[1
]}

Zonari, E. ^{[1
]}

Migliavacca, M. ^{[1
]}

Hernandez, R. Jofra ^{[1
]}

Scaramuzza, S. ^{[1
]}

Di Matteo, G. ^{[2
,3
]}

Sergi, L. Sergi ^{[1
]}

Kajaste-Rudnitski, A. ^{[1
]}

Trono, D. ^{[4
]}

Grez, M. ^{[5
]}

Rossi, P. ^{[2
,3
]}

Finocchi, A. ^{[2
,3
]}

Naldini, L. ^{[1
,6
]}

Gentner, B. ^{[1
]}

Aiuti, A. ^{[1
,2
,3
]}

机构：

[1] Sci Inst HS Raffaele Milan, San Raffaele Telethon Inst Gene Therapy TIGET, Milan, Italy

[2] Childrens Hosp Bambino Gesu, Dept Pediat, Rome, Italy

[3] Univ Roma Tor Vergata, Sch Med, Rome, Italy

[4] Ecole Polytech Fed Lausanne, Lausanne, Switzerland

[5] Georg Speyer Haus, Frankfurt, Germany

[6] Univ Vita Salute San Raffaele, Milan, Italy

来源：

HUMAN GENE THERAPY | 2014年 / 25卷 / 11期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

OR006

引用

页码：A26 / A26

页数：1

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[2] Dual-Regulated Lentiviral Vector for Gene Therapy of X-Linked Chronic Granulomatous Disease
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