ANTISENSE APPROACH FOR CF WITH NONSENSE MUTATIONS

被引：0
|
作者：
Huang, Lulu [1 ]
机构：
[1] Ionis Pharmaceut, Antisense Drug Discovery, Carlsbad, CA USA
来源：
PEDIATRIC PULMONOLOGY | 2019年 / 54卷
关键词：
OLIGONUCLEOTIDE;
D O I：
暂无
中图分类号：
R72 [儿科学];
学科分类号：
100202 ;
摘要：
S20.1
引用
下载
收藏
页码：S134 / S135
页数：2
相关论文
共 50 条
  • [1] Is antisense nonsense?
    Gertz, Morie A.
    LEUKEMIA & LYMPHOMA, 2009, 50 (04) : 519 - 520
  • [2] SENSE, NONSENSE AND ANTISENSE
    TANAKA, Y
    MACER, D
    TRENDS IN GENETICS, 1994, 10 (12) : 417 - 418
  • [3] Targeting Translation Termination Machinery with Antisense Oligonucleotides for Diseases Caused by Nonsense Mutations
    Huang, Lulu
    Aghajan, Mariam
    Quesenberry, Tianna
    Low, Audrey
    Murray, Susan F.
    Monia, Brett P.
    Guo, Shuling
    NUCLEIC ACID THERAPEUTICS, 2019, 29 (04) : 175 - 186
  • [4] ENGINEERED TRANSFER RNA APPROACH FOR NONSENSE-ASSOCIATED CF
    Porter, Joseph
    Ko, Wooree
    Edwards, Katherine
    Lueck, John D.
    PEDIATRIC PULMONOLOGY, 2019, 54 : S135 - S136
  • [5] SENSE, ANTISENSE, NONSENSE, AND MISSENSE
    CHENG, TO
    ANNALS OF THORACIC SURGERY, 1993, 56 (02): : 397 - 397
  • [6] Antisense suppression of the nonsense mediated decay factor Upf3b as a potential treatment for diseases caused by nonsense mutations
    Huang, Lulu
    Low, Audrey
    Damle, Sagar S.
    Keenan, Melissa M.
    Kuntz, Steven
    Murray, Susan F.
    Monia, Brett P.
    Guo, Shuling
    GENOME BIOLOGY, 2018, 19
  • [7] Antisense suppression of the nonsense mediated decay factor Upf3b as a potential treatment for diseases caused by nonsense mutations
    Lulu Huang
    Audrey Low
    Sagar S. Damle
    Melissa M. Keenan
    Steven Kuntz
    Susan F. Murray
    Brett P. Monia
    Shuling Guo
    Genome Biology, 19
  • [8] TARGETING CLASS 1 MUTATIONS: UPDATE ON ATALUREN AS A PROMISING TREATMENT FOR NONSENSE MUTATION CF
    Konstan, Michael
    Accurso, Frank
    De Boeck, Kris
    Kerem, Eitan
    Rowe, Steven
    Sermet-Gaudelus, Isabelle
    Wilschanski, Michael
    Barth, Jay
    Elfring, Gary
    Peltz, Stuart
    Ajayi, Temitayo
    PEDIATRIC PULMONOLOGY, 2012, 47 : 108 - 109
  • [9] UPREGULATION OF CFTR WITH NONSENSE MUTATIONS BY PROMOTING PTC READ-THROUGH OR MODULATING THE NONSENSE-MEDIATED DECAY PATHWAY WITH ANTISENSE OLIGONUCLEOTIDES
    Keenan, M. M.
    Huang, L.
    Guo, S.
    Monia, B. P.
    PEDIATRIC PULMONOLOGY, 2016, 51 : 201 - 202
  • [10] Not nonsense but antisense - Applications of antisense oligonucleotides in different fields of medicine
    Oberbauer, R
    WIENER KLINISCHE WOCHENSCHRIFT, 1997, 109 (02) : 40 - 46
12345