Oligonucleotide-based splice correction of the ABCA4 c.5461-10T>C mutation in Stargardt disease type 1

被引：0
|
作者：
Dulla, Kalyan [1 ]
Yilmaz-Elis, Seda [1 ]
Miao, Jiayi [1 ]
Schmidt, Iris [1 ]
Schulkens, Iris [1 ]
Chan, Hee Lam [1 ]
Adamson, Peter S. [1 ]
机构：
[1] ProQR Therapeut, Leiden, Netherlands
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2018年 / 59卷 / 09期
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暂无
中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
摘要：
5315
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页数：2
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