Optimization of Human FIX Expression Cassettes for Superior Liver-Targeted Gene Therapy of Hemophilia B

被引：0
|
作者：
Liu, Xiaojun [1 ]
Yamada, Kentaro [2 ]
Markusic, David M. [2 ]
Herzog, Roland W. [2 ]
Zhou, Pengcheng [1 ]
Zhang, Jason [1 ]
机构：
[1] Luye Boston Res & Dev LLC, GeneLeap Biotechnol LLC, Woburn, MA USA
[2] Indiana Univ, Dept Pediat, Gene & Cell Therapy Program, Herman B Wells Ctr Pediat Resear, Indianapolis, IN 46204 USA
来源：
MOLECULAR THERAPY | 2021年 / 29卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
340
引用
收藏
页码：168 / 168
页数：1
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