Immune modulation in a patient with Morquio syndrome treated with enzyme replacement therapy

被引:3
|
作者
Sun, Angela [1 ]
Alshuaibi, Walaa [2 ]
Petroni, Daniel [3 ]
Skoda-Smith, Suzanne [3 ]
Goldberg, Michael J. [4 ]
Hale, Susan [4 ]
机构
[1] Univ Washington, Sch Med, Dept Pediat, Div Genet Med, 4800 Sand Point Way NE,MB 8-632, Seattle, WA 98105 USA
[2] King Saud Univ, King Khalid Univ Hosp, Genet Unit, Dept Paediat, Riyadh, Saudi Arabia
[3] Univ Washington, Sch Med, Dept Pediat, Div Immunol, Seattle, WA 98105 USA
[4] Univ Washington, Sch Med, Dept Orthopaed & Sports Med, Seattle, WA USA
关键词
TOLERANCE INDUCTION;
D O I
10.1016/j.jaip.2017.12.024
中图分类号
R392 [医学免疫学];
学科分类号
100102 ;
摘要
[No abstract available]
引用
收藏
页码:1749 / 1751
页数:3
相关论文
共 50 条
  • [1] Immunomodulation in a patient with Morquio syndrome type A treated with enzyme replacement therapy
    Alshuaibi, Walaa
    Hale, Susan
    Petroni, Daniel
    Skoda-Smith, Suzanne
    Goldberg, Michael J.
    Sun, Angela
    MOLECULAR GENETICS AND METABOLISM, 2016, 117 (02) : S18 - S18
  • [2] Immune Modulation for Enzyme Replacement Therapy in A Female Patient With Hunter Syndrome
    Julien, Daniel C.
    Woolgar, Kara
    Pollard, Laura
    Miller, Holly
    Desai, Ankit
    Lindstrom, Kristin
    Kishnani, Priya S.
    FRONTIERS IN IMMUNOLOGY, 2020, 11
  • [3] Enzyme replacement therapy in a murine model of Morquio A syndrome
    Tomatsu, Shunji
    Montano, Adriana M.
    Ohashi, Amiko
    Gutierrez, Monica A.
    Oikawa, Hirotaka
    Oguma, Toshihiro
    Dung, Vu Chi
    Nishioka, Tatsuo
    Orii, Tadao
    Sly, William S.
    HUMAN MOLECULAR GENETICS, 2008, 17 (06) : 815 - 824
  • [4] Immune modulation in Pompe disease treated with enzyme replacement therapy
    Banugaria, Suhrad G.
    Patel, Trusha T.
    Kishnani, Priya S.
    EXPERT REVIEW OF CLINICAL IMMUNOLOGY, 2012, 8 (06) : 497 - 499
  • [5] ENZYME REPLACEMENT THERAPY: A CASE OF SUCCESSFUL ELOSULFASE ALFA DESENSITIZATION IN A MORQUIO A SYNDROME PATIENT.
    CaJacob, A.
    Adkins, C.
    Descartes, M.
    Allen, C.
    Anderson, J.
    ANNALS OF ALLERGY ASTHMA & IMMUNOLOGY, 2014, 113 (05) : A25 - A26
  • [6] Effect of enzyme replacement therapy on the growth of patients with Morquio syndrome type A
    Tomatsu, Shunji
    Doherty, Caitlin
    Stapleton, Molly
    MOLECULAR GENETICS AND METABOLISM, 2019, 126 (02) : S144 - S144
  • [7] Oral immunotherapy tolerizes mice to enzyme replacement therapy for Morquio A syndrome
    Sosa, Angela C.
    Kariuki, Barbara
    Gan, Qi
    Knutsen, Alan P.
    Bellone, Clifford J.
    Guzman, Miguel A.
    Barrera, Luis A.
    Tomatsu, Shunji
    Chauhan, Anil K.
    Armbrecht, Eric
    Montano, Adriana M.
    JOURNAL OF CLINICAL INVESTIGATION, 2020, 130 (03): : 1288 - 1300
  • [8] Enhancement of Drug Delivery: Enzyme-replacement Therapy for Murine Morquio A Syndrome
    Tomatsu, Shunji
    Montano, Adriana M.
    Dung, Vu Chi
    Ohashi, Amiko
    Oikawa, Hirotaka
    Oguma, Toshihiro
    Orii, Tadao
    Barrera, Luis
    Sly, William S.
    MOLECULAR THERAPY, 2010, 18 (06) : 1094 - 1102
  • [9] Aortic valve replacement in a patient with Morquio syndrome
    Nicolini, Francesco
    Corradi, Domenico
    Bosio, Silvia
    Gherli, Tiziano
    HEART SURGERY FORUM, 2008, 11 (02): : E96 - E98
  • [10] Effect of enzyme replacement therapy on the growth of patients with Morquio A
    Doherty, Caitlin
    Stapleton, Molly
    Piechnik, Matthew
    Mason, Robert W.
    Mackenzie, William G.
    Yamaguchi, Seiji
    Kobayashi, Hironori
    Suzuki, Yasuyuki
    Tomatsu, Shunji
    JOURNAL OF HUMAN GENETICS, 2019, 64 (07) : 625 - 635