Gene therapy results in long-term rescue of photoreceptor function in a mouse model for Bardet-Biedl Syndrome 1

被引：0
|
作者：
Freitas, M. M. Fernandes [4 ,5 ]
Hernandez-Hernandez, V. [1 ,2 ,3 ]
Pearson, R. A. [4 ,5 ]
Sidoli, C. [1 ]
Guillermin, O. [1 ]
Carreno, G. [1 ]
Cuevas, E. [1 ]
Smith, A. J. [4 ,5 ]
Ali, R. R. [4 ,5 ]
Beales, P. L. [1 ,3 ]
机构：
[1] Axovia Therapeut Inc, London, England
[2] Brunel Univ London, London, England
[3] UCL, Inst Child Hlth Great Ormond St, London, England
[4] UCL, Inst Ophthalmol, London, England
[5] Kings Coll London, London, England
来源：
HUMAN GENE THERAPY | 2021年 / 32卷 / 19-20期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P068
引用
收藏
页码：A49 / A49
页数：1
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