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- [1] Interim Results from a Phase 1/2 Clinical Study of Lentiglobin Gene Therapy for Severe Sickle Cell DiseaseBLOOD, 2016, 128 (22)Kanter, Julie论文数: 0 引用数: 0 h-index: 0机构: Med Univ S Carolina, Div Pediat, Charleston, SC USA Med Univ S Carolina, Div Pediat, Charleston, SC USAWalters, Mark C.论文数: 0 引用数: 0 h-index: 0机构: UCSF Benioff Childrens Hosp Oakland, Oakland, CA USA Med Univ S Carolina, Div Pediat, Charleston, SC USAHsieh, Matthew M.论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Mol & Clin Hematol Branch, NIDDK, NIH, Bethesda, MD USA Med Univ S Carolina, Div Pediat, Charleston, SC USA论文数: 引用数: h-index:机构:Kwiatkowski, Janet论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA USA Med Univ S Carolina, Div Pediat, Charleston, SC USAKamble, Rammurti T.论文数: 0 引用数: 0 h-index: 0机构: Baylor Coll Med, Ctr Cell & Gene Therapy, Houston, TX USA Houston Methodist Hosp, Houston, TX USA Med Univ S Carolina, Div Pediat, Charleston, SC USAvon Kalle, Christof论文数: 0 引用数: 0 h-index: 0机构: German Canc Res Ctr, Natl Ctr Tumor Dis NCT, Heidelberg, Germany Med Univ S Carolina, Div Pediat, Charleston, SC USAKuypers, Frans A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp, Oakland Res Inst, 747 52nd St, Oakland, CA 94609 USA Med Univ S Carolina, Div Pediat, Charleston, SC USACavazzana, Marina论文数: 0 引用数: 0 h-index: 0机构: Grp Hosp Univ Ouest, AP HP, Biotherapy Clin Invest Ctr, INSERM, Paris, France Med Univ S Carolina, Div Pediat, Charleston, SC USA论文数: 引用数: h-index:机构:Joseney-Antoine, Marcelyne论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio, Cambridge, MA USA Med Univ S Carolina, Div Pediat, Charleston, SC USAAsmal, Mohammed论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio, Cambridge, MA USA Med Univ S Carolina, Div Pediat, Charleston, SC USAThompson, Alexis A.论文数: 0 引用数: 0 h-index: 0机构: Ann Robert H Lurie Childrens Hosp Chicago, Div Hematol Oncol Stem Cell Transplant, Chicago, IL USA Med Univ S Carolina, Div Pediat, Charleston, SC USATisdale, John F.论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Mol & Clin Hematol Branch, NIDDK, NIH, Bethesda, MD USA Med Univ S Carolina, Div Pediat, Charleston, SC USA
- [2] LentiGlobin Gene Therapy in Patients with Sickle Cell Disease: Updated Interim Results from HGB-206MOLECULAR THERAPY, 2019, 27 (04) : 1 - 1Tisdale, John F.论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA论文数: 引用数: h-index:机构:Mapara, Markus Y.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAKwiatkowski, Janet L.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA论文数: 引用数: h-index:机构:Schmidt, Manfred论文数: 0 引用数: 0 h-index: 0机构: GeneWerk GmbH, Heidelberg, Germany NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAMiller, Alexandra L.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAPierciey, Francis J.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAShi, Weiliang论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USARibeil, Jean-Antoine论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAAsmal, Mohammed论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAThompson, Alexis A.论文数: 0 引用数: 0 h-index: 0机构: Ann & Robert H Lurie Childrens Hosp Chicago, Chicago, IL 60611 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAWalters, Mark C.论文数: 0 引用数: 0 h-index: 0机构: UCSF Benioff Childrens Hosp Oakland, Oakland, CA USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA
- [3] Lentiglobin gene therapy in patients with sickle cell disease: Updated interim results from HGB-206BONE MARROW TRANSPLANTATION, 2019, 54 : 77 - 78Mapara, Markus Y.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USATisdale, John F.论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USA论文数: 引用数: h-index:机构:Kwiatkowski, Janet L.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USAKrishnamurti, Lakshmanan论文数: 0 引用数: 0 h-index: 0机构: Emory Sch Med, Atlanta, GA USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USASchmidt, Manfred论文数: 0 引用数: 0 h-index: 0机构: GeneWerk GmbH, Heidelberg, Germany Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USAMiller, Alexandra L.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USAPierciey, Francis J., Jr.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USAShi, Weiliang论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USARibeil, Jean-Antoine论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USAAsmal, Mohammed论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USAThompson, Alexis A.论文数: 0 引用数: 0 h-index: 0机构: Ann & Robert H Lurie Childrens Hosp Chicago, Chicago, IL 60611 USA Northwestern Univ, Chicago, IL 60611 USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USAWalters, Mark论文数: 0 引用数: 0 h-index: 0机构: UCSF Benioff Childrens Hosp Oakland, Oakland, CA USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USA
- [4] LentiGlobin Gene Therapy in Patients with Sickle Cell Disease: Updated Interim Results from HGB-206BRITISH JOURNAL OF HAEMATOLOGY, 2019, 185 : 22 - 23Thompson, A. A.论文数: 0 引用数: 0 h-index: 0机构: Ann & Robert H Lurie Childrens Hosp, Pediat Hematol, Chicago, IL USA Ann & Robert H Lurie Childrens Hosp, Pediat Hematol, Chicago, IL USATisdale, J. F.论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA Ann & Robert H Lurie Childrens Hosp, Pediat Hematol, Chicago, IL USA论文数: 引用数: h-index:机构:Mapara, M. Y.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USA Ann & Robert H Lurie Childrens Hosp, Pediat Hematol, Chicago, IL USAKwiatkowski, J. L.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA Ann & Robert H Lurie Childrens Hosp, Pediat Hematol, Chicago, IL USAKrishnamurti, L.论文数: 0 引用数: 0 h-index: 0机构: Emory Sch Med, Div Hematol Oncol BMT, Dept Pediat, Atlanta, GA USA Ann & Robert H Lurie Childrens Hosp, Pediat Hematol, Chicago, IL USASchmidt, M.论文数: 0 引用数: 0 h-index: 0机构: GeneWerk GmbH, Heidelberg, Germany Ann & Robert H Lurie Childrens Hosp, Pediat Hematol, Chicago, IL USAMiller, A.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Ann & Robert H Lurie Childrens Hosp, Pediat Hematol, Chicago, IL USAPierciey, F. J.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Ann & Robert H Lurie Childrens Hosp, Pediat Hematol, Chicago, IL USAShi, W.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Ann & Robert H Lurie Childrens Hosp, Pediat Hematol, Chicago, IL USARibeil, J. -A.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Ann & Robert H Lurie Childrens Hosp, Pediat Hematol, Chicago, IL USAAsmal, M.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Ann & Robert H Lurie Childrens Hosp, Pediat Hematol, Chicago, IL USAWalters, M. C.论文数: 0 引用数: 0 h-index: 0机构: UCSF Benioff Childrens Hosp Oakland, Hematol Oncol BMT, Oakland, CA USA Ann & Robert H Lurie Childrens Hosp, Pediat Hematol, Chicago, IL USA
- [5] Lentiglobin Gene Therapy in Patients with Sickle Cell Disease: Updated Interim Results from Hgb-206BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION, 2019, 25 (03)Mapara, Markus Y.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USATisdale, John F.论文数: 0 引用数: 0 h-index: 0机构: NIDDK, Sickle Cell Branch, NHLBI, NIH, Bethesda, MD 20892 USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USA论文数: 引用数: h-index:机构:Kwiatkowski, Janet L.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USAKrishnamurti, Lakshmanan论文数: 0 引用数: 0 h-index: 0机构: Emory Sch Med, Div Hematol Oncol BMT, Dept Pediat, Atlanta, GA USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USASchmidt, Manfred论文数: 0 引用数: 0 h-index: 0机构: GeneWerk GmbH, Heidelberg, Germany Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USAMiller, Alexandra L.论文数: 0 引用数: 0 h-index: 0机构: Bluebird bio Inc, Cambridge, MA USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USAPierciey, Francis J., Jr.论文数: 0 引用数: 0 h-index: 0机构: Bluebird bio Inc, Cambridge, MA USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USAShi, Weiliang论文数: 0 引用数: 0 h-index: 0机构: Bluebird bio Inc, Cambridge, MA USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USARibeil, Jean-Antoine论文数: 0 引用数: 0 h-index: 0机构: Bluebird bio Inc, Cambridge, MA USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USAAsmal, Mohammed论文数: 0 引用数: 0 h-index: 0机构: Bluebird bio Inc, Cambridge, MA USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USAThompson, Alexis A.论文数: 0 引用数: 0 h-index: 0机构: Ann & Robert H Lurie Childrens Hosp, Pediat Hematol, Chicago, IL USA Northwestern Univ, Feinberg Sch Med, Chicago, IL 60611 USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USAWalters, Mark C.论文数: 0 引用数: 0 h-index: 0机构: UCSF Benioff Childrens Hosp, Hematol Oncol BMT, Oakland, CA USA Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USA
- [6] Results from the Completed Hgb-205 Trial of Lentiglobin for β-Thalassemia and Lentiglobin for Sickle Cell Disease Gene TherapyBLOOD, 2019, 134Magrin, Elisa论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, France Necker Assistance Publ Hop Paris, Biotherapy Dept, Paris, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceSemeraro, Michaela论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceMagnani, Alessandra论文数: 0 引用数: 0 h-index: 0机构: Necker Enfants Malad Univ Hosp, Paris, France Grp Hosp Univ Ouest, Assistance Publ Hop Paris, Biotherapy Clin Invest Ctr, Paris, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, France论文数: 引用数: h-index:机构:Miccio, Annarita论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 05, IMAGINE Inst, Sorbonne Paris Cite, Paris, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceHebert, Nicolas论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Est Creteil, Creteil, France Hop Henri Mondor, Etab Francais Sang, Creteil, France Univ Paris Est Creteil, Inst Mondor, Lab Excellence GR Ex, INSERM U955,EFS,Team Transfus & Malad Globule Rou, Creteil, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceDiana, Jean-Sebastien论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceLefrere, Francois论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceSuarez, Felipe论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceHermine, Olivier论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceBrousse, Valentine论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FrancePoirot, Catherine论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceBourget, Philippe论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceEl Nemer, Wassim论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceGuichard, Isabelle论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceMoshous, Despina论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceNeven, Benedicte论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 05, IMAGINE Inst, Sorbonne Paris Cite, Paris, France Hop Necker Enfants Malad, Paris, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceMonpoux, Fabrice论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Nice, Nice, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FrancePoiree, Marilyne论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Nice, Nice, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceBartolucci, Pablo论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Est Creteil, Inst Mondor, Lab Excellence GR Ex, INSERM U955,EFS,Team Transfus & Malad Globule Rou, Creteil, France Henri Mondor Hosp, APHP, Creteil, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceMeritet, Jean-Francois论文数: 0 引用数: 0 h-index: 0机构: Hop Cochin St Vincent Paul, Paris, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceGrevent, David论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, Dept Pediat Neuroradiol, Paris, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceLefebvre, Thibaud论文数: 0 引用数: 0 h-index: 0机构: Univ Paris, Louis Mourier Hosp, Assistance Publ Hop Paris, Paris, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceAsmal, Mohammed论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceWhitney, Erin论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceGayron, Marisa论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceHuang, Wenmei论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceFunck-Brentano, Isabelle论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, Francede Montalembert, Mariane论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, APHP, Referral Ctr Sickle Cell Dis, Pediat, Paris, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceJoseph, Laure论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, Assistance Publ Hop Paris, Biotherapy Dept, Paris, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceRibeil, Jean-Antoine论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, FranceCavazzana, Marina论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Grp Hosp Univ Ouest, Biotherapy Clin Invest Ctr, Paris, France Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, France
- [7] Current Results of Lentiglobin Gene Therapy in Patients with Severe Sickle Cell Disease Treated Under a Refined Protocol in the Phase 1 Hgb-206 StudyBLOOD, 2018, 132Tisdale, John F.论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA论文数: 引用数: h-index:机构:Mapara, Markus Y.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ Coll Phys & Surg, 630 W 168th St, New York, NY 10032 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAKwiatkowski, Janet L.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA论文数: 引用数: h-index:机构:Schmidt, Manfred论文数: 0 引用数: 0 h-index: 0机构: GeneWerk GmbH, Heidelberg, Germany NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAMiller, Alexandra L.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAPierciey, Francis J., Jr.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAShi, Weiliang论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USARibeil, Jean-Antoine论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAAsmal, Mohammed论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAThompson, Alexis A.论文数: 0 引用数: 0 h-index: 0机构: Ann & Robert H Lurie Childrens Hosp Chicago, Chicago, IL 60611 USA Northwestern Univ, Feinberg Sch Med, Chicago, IL 60611 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAWalters, Mark C.论文数: 0 引用数: 0 h-index: 0机构: UCSF Benioff Childrens Hosp, Oakland, CA USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA
- [8] LENTIGLOBIN GENE THERAPY FOR PATIENTS WITH SICKLE CELL DISEASE: UPDATED RESULTS FROM STUDY HGB-206PEDIATRIC BLOOD & CANCER, 2020, 67 : S32 - S32Thompson, Alexis论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAKrishnamurti, Lakshmanan论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAMapara, Markus论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAKwiatkowski, Janet论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USATisdale, John论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USASchmidt, Manfred论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAMiller, Alexandra论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAPierciey, Francis, Jr.论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAHuang, Wenmei论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USARibeil, Jean-Antoine论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAKanter, Julie论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USAWalters, Mark论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA
- [9] Lentiglobin for Sickle Cell Disease (SCD) Gene Therapy (GT): Updated Results in Group C Patients from the Phase 1/2 HGB-206 StudyBONE MARROW TRANSPLANTATION, 2020, 55 (SUPPL 1) : 78 - 79Mapara, Markus Y.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Coll Phys & Surg, New York, NY USA Columbia Univ, Coll Phys & Surg, New York, NY USATisdale, John F.论文数: 0 引用数: 0 h-index: 0机构: NIH, Bethesda, MD USA Columbia Univ, Coll Phys & Surg, New York, NY USA论文数: 引用数: h-index:机构:Kwiatkowski, Janet L.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Philadelphia, PA 19104 USA Columbia Univ, Coll Phys & Surg, New York, NY USAKrishnamurti, Lakshmanan论文数: 0 引用数: 0 h-index: 0机构: Emory Sch Med, Atlanta, GA USA Columbia Univ, Coll Phys & Surg, New York, NY USASchmidt, Manfred论文数: 0 引用数: 0 h-index: 0机构: GeneWerk GmbH, Heidelberg, Germany Columbia Univ, Coll Phys & Surg, New York, NY USAMiller, Alexandra L.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Columbia Univ, Coll Phys & Surg, New York, NY USAPierciey, Francis J., Jr.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Columbia Univ, Coll Phys & Surg, New York, NY USABonner, Melissa论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Columbia Univ, Coll Phys & Surg, New York, NY USAHuang, Wenmei论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Columbia Univ, Coll Phys & Surg, New York, NY USARibeil, Jean-Antoine论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA Columbia Univ, Coll Phys & Surg, New York, NY USAThompson, Alexis A.论文数: 0 引用数: 0 h-index: 0机构: Northwestern Univ, Ann & Robert H Lurie Childrens Hosp Chicago, Chicago, IL 60611 USA Columbia Univ, Coll Phys & Surg, New York, NY USAWalters, Mark C.论文数: 0 引用数: 0 h-index: 0机构: UCSF Benioff Childrens Hosp, Oakland, CA USA Columbia Univ, Coll Phys & Surg, New York, NY USA
- [10] Lentiglobin for Sickle Cell Disease (SCD) Gene Therapy (GT): Updated Results in Group C Patients from the Phase 1/2 Hgb-206 StudyBIOLOGY OF BLOOD AND MARROW TRANSPLANTATION, 2020, 26 (03) : S1 - S2Walters, Mark C.论文数: 0 引用数: 0 h-index: 0机构: UCSF Benioff Childrens Hosp, Hematol Oncol Dept, Oakland, CA USA UCSF Benioff Childrens Hosp, Hematol Oncol Dept, Oakland, CA USA论文数: 引用数: h-index:机构:Kwiatkowski, Janet L.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USA UCSF Benioff Childrens Hosp, Hematol Oncol Dept, Oakland, CA USA论文数: 引用数: h-index:机构:Mapara, Markus Y.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ Coll Phys & Surg, Dept Med, New York, NY USA UCSF Benioff Childrens Hosp, Hematol Oncol Dept, Oakland, CA USASchmidt, Manfred论文数: 0 引用数: 0 h-index: 0机构: GeneWerk GmbH, Heidelberg, Germany UCSF Benioff Childrens Hosp, Hematol Oncol Dept, Oakland, CA USAMiller, Alexandra L.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA UCSF Benioff Childrens Hosp, Hematol Oncol Dept, Oakland, CA USAPierciey, Jr. Francis J.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA UCSF Benioff Childrens Hosp, Hematol Oncol Dept, Oakland, CA USABonner, Melissa论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA UCSF Benioff Childrens Hosp, Hematol Oncol Dept, Oakland, CA USAHuang, Wenmei论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA UCSF Benioff Childrens Hosp, Hematol Oncol Dept, Oakland, CA USARibeil, Jean-Antoine论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Cambridge, MA USA UCSF Benioff Childrens Hosp, Hematol Oncol Dept, Oakland, CA USAThompson, Alexis A.论文数: 0 引用数: 0 h-index: 0机构: Ann & Robert H Lurie Childrens Hosp Chicago, Chicago, IL 60611 USA Northwestern Univ, Feinberg Sch Med, Pediat Hematol Oncol & Stem Cell Transplantat, Chicago, IL 60611 USA UCSF Benioff Childrens Hosp, Hematol Oncol Dept, Oakland, CA USATisdale, John F.论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Sickle Cell Branch, NIDDK, NIH, Bldg 10, Bethesda, MD 20892 USA UCSF Benioff Childrens Hosp, Hematol Oncol Dept, Oakland, CA USA