An AAV vector toolbox for CRISPR/Cas9-mediated genome engineering

被引:0
|
作者
Senis, Elena [1 ]
Fatouros, Chronis [1 ]
Grosse, Stefanie [1 ]
Wiedtke, Ellen [1 ]
Niopek, Dominik [3 ]
Mueller, Ann-Kristin [2 ]
Boerner, Kathleen [1 ]
Grimm, Dirk [1 ]
机构
[1] Univ Heidelberg Hosp, Dept Infect Dis, Cluster Excellence CellNetworks, Heidelberg, Germany
[2] Univ Heidelberg Hosp, Dept Infect Dis, Heidelberg, Germany
[3] German Canc Res Ctr, Div Theoret Bioinformat, Heidelberg, Germany
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
OR002
引用
收藏
页码:A24 / A25
页数:2
相关论文
共 50 条
  • [1] CRISPR/Cas9-mediated genome engineering: An adeno-associated viral (AAV) vector toolbox
    Senis, Elena
    Fatouros, Chronis
    Grosse, Stefanie
    Wiedtke, Ellen
    Niopek, Dominik
    Mueller, Ann-Kristin
    Boerner, Kathleen
    Grimm, Dirk
    BIOTECHNOLOGY JOURNAL, 2014, 9 (11) : 1402 - 1412
  • [2] CRISPR/Cas9-mediated genome engineering of the ferret
    Zhaohui Kou
    Qian Wu
    Xiaochen Kou
    Chonghai Yin
    Hong Wang
    Zhentao Zuo
    Yan Zhuo
    Antony Chen
    Shaorong Gao
    Xiaoqun Wang
    Cell Research, 2015, 25 : 1372 - 1375
  • [3] CRISPR/Cas9-mediated genome engineering of the ferret
    Kou, Zhaohui
    Wu, Qian
    Kou, Xiaochen
    Yin, Chonghai
    Wang, Hong
    Zuo, Zhentao
    Zhuo, Yan
    Chen, Antony
    Gao, Shaorong
    Wang, Xiaoqun
    CELL RESEARCH, 2015, 25 (12) : 1372 - 1375
  • [4] CRISPR/Cas9-mediated genome editing via postnatal administration of AAV vector cures haemophilia B mice
    Tsukasa Ohmori
    Yasumitsu Nagao
    Hiroaki Mizukami
    Asuka Sakata
    Shin-ichi Muramatsu
    Keiya Ozawa
    Shin-ichi Tominaga
    Yutaka Hanazono
    Satoshi Nishimura
    Osamu Nureki
    Yoichi Sakata
    Scientific Reports, 7
  • [5] CRISPR/Cas9-mediated genome editing via postnatal administration of AAV vector cures haemophilia B mice
    Ohmori, Tsukasa
    Nagao, Yasumitsu
    Mizukami, Hiroaki
    Sakata, Asuka
    Muramatsu, Shin-ichi
    Ozawa, Keiya
    Tominaga, Shin-ichi
    Hanazono, Yutaka
    Nishimura, Satoshi
    Nureki, Osamu
    Sakata, Yoichi
    SCIENTIFIC REPORTS, 2017, 7
  • [6] CRISPR/Cas9-mediated base editors and their prospects for mitochondrial genome engineering
    Eghbalsaied, Shahin
    Lawler, Clancy
    Petersen, Bjorn
    Hajiyev, Raul A.
    Bischoff, Steve R.
    Frankenberg, Stephen
    GENE THERAPY, 2024, 31 (5-6) : 209 - 223
  • [7] CRISPR/Cas9-mediated genome engineering and the promise of designer flies on demand
    Gratz, Scott J.
    Wildonger, Jill
    Harrison, Melissa M.
    O'Connor-Giles, Kate M.
    FLY, 2013, 7 (04) : 249 - 255
  • [8] Off-target Effects in CRISPR/Cas9-mediated Genome Engineering
    Zhang, Xiao-Hui
    Tee, Louis Y.
    Wang, Xiao-Gang
    Huang, Qun-Shan
    Yang, Shi-Hua
    MOLECULAR THERAPY-NUCLEIC ACIDS, 2015, 4 : e264
  • [9] CRISPR/Cas9-mediated base editors and their prospects for mitochondrial genome engineering
    Shahin Eghbalsaied
    Clancy Lawler
    Björn Petersen
    Raul A. Hajiyev
    Steve R. Bischoff
    Stephen Frankenberg
    Gene Therapy, 2024, 31 : 209 - 223
  • [10] Mosaicism in CRISPR/Cas9-mediated genome editing
    Mehravar, Maryam
    Shirazi, Abolfazl
    Nazari, Mahboobeh
    Banan, Mehdi
    DEVELOPMENTAL BIOLOGY, 2019, 445 (02) : 156 - 162