Multicenter, non-interventional, double cohort study to assess the safety of alglucosidase alfa and laronidase in real-world home infusion setting

被引：0

作者：

Toscano, Antonio ^{[1
]}

Scarpa, Maurizio ^{[2
]}

Parini, Rossella ^{[3
]}

Donati, Alice ^{[4
]}

Crescimanno, Grazia ^{[5
]}

Fiumara, Agata ^{[6
,7
]}

Fischetto, Rita ^{[8
]}

Gasperini, Serena

Siciliano, Gabriele ^{[9
]}

Ravaglia, Sabrina ^{[10
]}

Sechi, Annalisa

Piperno, Alberto ^{[11
]}

Cianci, Vittorio ^{[12
]}

Maggi, Lorenzo ^{[13
]}

Musumeci, Olimpia

Taurisano, Roberta

Verrecchia, Elena ^{[14
]}

机构：

[1] Policlin Univ Gaetano Martino, Messina, Italy

[2] Univ Friuli, Cent Presidio Osped S Maria Misericordia, Ctr Coordinamento Reg Malattie Rare Azienda Sanit, Udine, Italy

[3] Univ Milano Bicocca, Fdn Monza & Brianza, Osped San Gerardo Monza Clin Pediatr, Monza, Italy

[4] DH Malattie Metabol Muscolariereditarie Osped, Piano Terra DH, Florence, Italy

[5] AO Villa Sofia Cervello, UO Malattie Apparato Resp, Palermo, Italy

[6] UO Clin Pediatr, AO Policlinico Vittorio Emanuele, Catania, Italy

[7] Ctr Riferimento Reg Malattie Metabol Congenite In, Catania, Italy

[8] Policlin Bari Stabilimento Pediatr Giovanni XXIII, Bari, Italy

[9] Univ Pisa, Dipartimento Med Clin & Sperimentale, Ospedale S Chiara, Pisa, Italy

[10] IIRCCS Fdn Ist Neurol Nazl C Mondino, Pavia, Italy

[11] Univ Milan, Osped San Gerardo Monza, Bicocca ASST Monza, Ctr Malattie Rare, Monza, Italy

[12] Grande Osped Metropolitano Bianchi Melacrino Mor, Reggio Di Calabria, Italy

[13] Osped Pediatr Bambin Gesu, Rome, Italy

[14] Policlin Gemelli, Rome, Italy

来源：

MOLECULAR GENETICS AND METABOLISM | 2022年 / 135卷 / 02期

关键词：

D O I：

10.1016/j.ymgme.2021.11.319

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

304

引用

页码：S120 / S120

页数：1

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