CAP-001: Systemic AAV Gene Therapy with Next Generation Capsids for MPS II Disease

被引：0

作者：

Ou, Li ^{[1
]}

Octeau, Christopher ^{[1
]}

Bonet, Bailey ^{[1
]}

Lam, Kevin ^{[1
]}

Siemian, Justin ^{[1
]}

Dreher, Renee ^{[1
]}

Roxas, Kristina ^{[1
]}

Jeffreys, David ^{[1
]}

Thomas, Shelby ^{[1
]}

Grepo, Nicole ^{[1
]}

Sandrock, Robert ^{[1
]}

Cockrell, Adam ^{[1
]}

Scherrer, Jon ^{[1
]}

Ressler, Reed ^{[1
]}

Wheeler, Brandon ^{[1
]}

Badger, Drew ^{[1
]}

Knoll, Allison ^{[1
]}

Goeden, Nick ^{[1
]}

机构：

[1] Capsida Biotherapeut Inc, Thousand Oaks, CA USA

来源：

MOLECULAR THERAPY | 2022年 / 30卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

471

引用

页码：223 / 223

页数：1

共 44 条

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