Iduronidase-transposed human B lymphocytes correct enzyme deficiency and glycosaminoglycan storage disease in immunodeficient mucopolysaccharidosis type I mice

被引：0
|
作者：
Hampe, Christiane S. [1 ]
Meeker, Kole D. [1 ]
Swietlicka, Monika [1 ]
Olson, Erik R. [2 ]
Lund, Troy C. [3 ]
Wesley, Jacob [1 ]
McIvor, R. S. [2 ]
机构：
[1] Immusoft, Seattle, WA USA
[2] Immusoft, Minneapolis, MN USA
[3] Univ Minnesota, Minneapolis, MN USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2022年 / 135卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2021.11.129
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
114
引用
收藏
页码：S53 / S53
页数：1
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