Novel RNA-Targeting Gene Therapy Approach for Usher's Syndrome Type II Retinitis Pigmentosa

被引:0
|
作者
Gibbs, Daniel [1 ]
Lardelli, Rea [1 ]
Nacthrab, Greg [1 ]
Roth, Daniela M. [1 ]
Lee, Shawn [1 ]
Geddes, Claire [1 ]
Wilson, Alistair [1 ]
Narayan, Nandini [1 ]
Zisoulis, Dimitrios [1 ]
Batra, Ranjan [1 ]
机构
[1] Locanabio Inc, San Diego, CA USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
100
引用
收藏
页码:50 / 50
页数:1
相关论文
共 50 条
  • [1] Towards a clinical trial of gene therapy for Usher syndrome type IB retinitis pigmentosa
    Dell'Aquila, F.
    Ferla, R.
    Trapani, I.
    Doria, M.
    Ferraiuolo, M.
    Iodice, C.
    Colloca, S.
    Auricchio, A.
    HUMAN GENE THERAPY, 2019, 30 (11) : A108 - A108
  • [2] Towards a Clinical Trial of Gene Therapy for Retinitis Pigmentosa Associated with Usher Syndrome Type IB
    Ferla, Rita
    Dell'Aquila, Fabio
    Doria, Monica
    Trapani, Ivana
    Ferraiuolo, Maria
    Noto, Alessia
    Grazioli, Fabiana
    Ammendola, Virginia
    Colloca, Stefano
    Auricchio, Alberto
    MOLECULAR THERAPY, 2021, 29 (04) : 131 - 132
  • [3] Towards a clinical trial of gene therapy to target retinitis pigmentosa associated with Usher syndrome type IB
    Ferla, R.
    Dell'Aquila, F.
    Doria, M.
    Ferraiuolo, M.
    Noto, A.
    Grazioli, F.
    Ammendola, V.
    Colloca, S.
    Auricchio, A.
    HUMAN GENE THERAPY, 2021, 32 (19-20) : A75 - A75
  • [4] Photodynamic therapy for vasoproliferative tumour associated with retinitis pigmentosa and Usher syndrome type 2
    Grassi, Piergiacomo
    CLINICAL AND EXPERIMENTAL OPTOMETRY, 2022, 105 (01) : 91 - 93
  • [5] Choroidal melanoma in a patient with retinitis pigmentosa and Usher's syndrome
    Gündüz, K
    Shields, JA
    Shields, CL
    Zhao, DY
    BRITISH JOURNAL OF OPHTHALMOLOGY, 1998, 82 (07) : 847 - 848
  • [6] Seven novel mutations in the long isoform of the USH2A gene in Chinese families with nonsyndromic retinitis pigmentosa and Usher syndrome Type II
    Xu, Wenjun
    Dai, Hanjun
    Lu, Tingting
    Zhang, Xiaohui
    Dong, Bing
    Li, Yang
    MOLECULAR VISION, 2011, 17 (172-74): : 1537 - 1552
  • [7] Novel mutations in the long isoform of the USH2A gene in patients with Usher syndrome type II or non-syndromic retinitis pigmentosa
    McGee, Terri L.
    Seyedahmadi, Babak Jian
    Sweeney, Meredith O.
    Dryja, Thaddeus P.
    Berson, Eliot L.
    JOURNAL OF MEDICAL GENETICS, 2010, 47 (07) : 499 - 506
  • [8] Novel deletions involving the USH2A gene in patients with Usher syndrome and retinitis pigmentosa
    Garcia-Garcia, Gema
    Aller, Elena
    Jaijo, Teresa
    Aparisi, Maria J.
    Larrieu, Lise
    Faugere, Valerie
    Blanco-Kelly, Fiona
    Ayuso, Carmen
    Roux, Anne-Francoise
    Millan, Jose M.
    MOLECULAR VISION, 2014, 20 : 1398 - 1410
  • [9] PHOSDUCIN AS A CANDIDATE GENE FOR RETINITIS-PIGMENTOSA AND USHER SYNDROME TYPEII
    ARA, F
    JACOBSON, S
    INANA, G
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 1993, 34 (04) : 1458 - 1458
  • [10] USH3A mutations in patients with a prior diagnosis of Usher syndrome type 1, Usher syndrome type II, and nonsyndromic recessive retinitis pigmentosa
    Seyedahmadi, BJ
    Berson, EL
    Dryja, T
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2004, 45 : U509 - U509