Liver-directed gene therapy with lentiviral vectors achieve normal levels of clotting factor VIII and IX in non-human primates

被引：0
|
作者：
Milani, M. [1 ]
Canepari, C. [1 ]
Annoni, A. [1 ]
Liu, T. [3 ]
Plati, T. [1 ]
Biffi, M. [1 ]
Russo, F. [1 ]
Patarroyo-White, S. [3 ]
Drager, D. [3 ]
Ayuso, E. [4 ]
Peters, R. [3 ]
Naldini, L. [1 ,2 ]
Cantore, A. [1 ,2 ]
机构：
[1] San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy
[2] Vita Salute San Raffaele Univ, Milan, Italy
[3] Sanofi, Paris, France
[4] Univ Nantes, INSERM, UMR 1089, Nantes, France
来源：
HUMAN GENE THERAPY | 2019年 / 30卷 / 11期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P201
引用
收藏
页码：A77 / A77
页数：1
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