A Novel AAV8 Vector for Microdystrophin Gene Therapy of Duchenne Muscular Dystrophy: Preclinical Studies in the Mdx Mouse

被引：0
|
作者：
Kim, SunJung [1 ]
Buss, Nicholas [1 ]
Patel, Hiren [1 ]
Yang, Lin [1 ]
Elliott, Kirk [1 ]
Qiao, Chunping [1 ]
Liu, Ye [1 ]
Fiscella, Michele [1 ]
Danos, Olivier [1 ]
机构：
[1] REGENXBIO Inc, Rockville, MD USA
来源：
MOLECULAR THERAPY | 2021年 / 29卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
614
引用
收藏
页码：297 / 298
页数：2
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