Etranacogene Dezaparvovec (AAV5-Padua hFIX variant), an Enhanced Vector for Gene Transfer in Adults with Severe or Moderate-Severe Hemophilia B: Two Year Data from a Phase 2b Trial

被引：0
|
作者：
von Drygalski, Annette
Giermasz, Adam
Castaman, Giancarlo
Key, Nigel S.
Lattimore, Susan U.
Leebeek, Frank W. G.
Miesbach, Wolfgang A.
Recht, Michael
Gomez, Esteban
Gut, Robert
Pipe, Steven W.
机构：
来源：
BLOOD | 2020年 / 136卷
关键词：
D O I：
10.1182/blood-2020-139295
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
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页数：3
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