共 50 条
- [1] AAV Therapy Attenuates Respiratory Dysfunction and Glycogen Accumulation in a Murine Model of Glycogen Storage Disease Type IIMOLECULAR THERAPY, 2015, 23 : S159 - S159Falk, Darin J.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Pediat, Gainesville, FL USA Univ Florida, Pediat, Gainesville, FL USASoustek, Meghan S.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Pediat, Gainesville, FL USA Univ Florida, Pediat, Gainesville, FL USATodd, A. Gary论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Pediat, Gainesville, FL USA Univ Florida, Pediat, Gainesville, FL USAMah, Cathryn S.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Pediat, Gainesville, FL USA Univ Florida, Pediat, Gainesville, FL USACloutier, Denise A.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Pediat, Gainesville, FL USA Univ Florida, Pediat, Gainesville, FL USAClement, Nathalie论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Pediat, Gainesville, FL USA Univ Florida, Pediat, Gainesville, FL USAFuller, David D.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Phys Therapy, Gainesville, FL USA Univ Florida, Pediat, Gainesville, FL USAByrne, Barry J.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Pediat, Gainesville, FL USA Univ Florida, Pediat, Gainesville, FL USA
- [2] AAV9 Attenuates Neuromuscular Pathology in Pompe DiseaseMOLECULAR THERAPY, 2014, 22 : S155 - S155Todd, A. Gary论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAMcElroy, Jessica A.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAGrange, Robert W.论文数: 0 引用数: 0 h-index: 0机构: Virginia Tech, Blacksburg, VA USA Univ Florida, Gainesville, FL USAFuller, David D.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAWalter, Glenn A.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAByrne, Barry J.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USADarin, Falk J.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USA
- [3] Treatment of infantile-onset Pompe disease in a rat model with muscle-directed AAV gene therapyMOLECULAR METABOLISM, 2024, 81Munoz, Sergio论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra 08193, Spain Inst Salud Carlos III, Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainBertolin, Joan论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra 08193, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainJimenez, Veronica论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra 08193, Spain Inst Salud Carlos III, Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainJaen, Maria Luisa论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra 08193, Spain Inst Salud Carlos III, Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainGarcia, Miquel论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra 08193, Spain Inst Salud Carlos III, Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainPujol, Anna论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra 08193, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainVila, Laia论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra 08193, Spain Inst Salud Carlos III, Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainSacristan, Victor论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra 08193, Spain Inst Salud Carlos III, Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainBarbon, Elena论文数: 0 引用数: 0 h-index: 0机构: Univ Evry, Univ Paris Saclay, INTEGRARE, Genethon,INSERM,UMR951, F-91002 Evry, France Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainRonzitti, Giuseppe论文数: 0 引用数: 0 h-index: 0机构: Univ Evry, Univ Paris Saclay, INTEGRARE, Genethon,INSERM,UMR951, F-91002 Evry, France Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainEl Andari, Jihad论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ, Med Fac, BioQuant Ctr, Dept Infect Dis Virol,Sect Viral Vector Technol, D-69120 Heidelberg, Germany Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainTulalamba, Warut论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ Brussel VUB, Dept Gene Therapy & Regenerat Med, B-1090 Brussels, Belgium Univ Leuven, Ctr Mol & Vasc Biol, Dept Cardiovasc Sci, B-3000 Leuven, Belgium Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainPham, Quang Hong论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ Brussel VUB, Dept Gene Therapy & Regenerat Med, B-1090 Brussels, Belgium Univ Leuven, Ctr Mol & Vasc Biol, Dept Cardiovasc Sci, B-3000 Leuven, Belgium Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainRuberte, Jesus论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Anim Hlth & Anat, Bellaterra 08193, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainVandenDriessche, Thierry论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ Brussel VUB, Dept Gene Therapy & Regenerat Med, B-1090 Brussels, Belgium Univ Leuven, Ctr Mol & Vasc Biol, Dept Cardiovasc Sci, B-3000 Leuven, Belgium Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainChuah, Marinee K.论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ Brussel VUB, Dept Gene Therapy & Regenerat Med, B-1090 Brussels, Belgium Univ Leuven, Ctr Mol & Vasc Biol, Dept Cardiovasc Sci, B-3000 Leuven, Belgium Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainGrimm, Dirk论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ, Med Fac, BioQuant Ctr, Dept Infect Dis Virol,Sect Viral Vector Technol, D-69120 Heidelberg, Germany German Ctr Infect Res DZIF, Heidelberg, Germany German Ctr Cardiovasc Res DZHK, Partner Site Heidelberg, Heidelberg, Germany Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainMingozzi, Federico论文数: 0 引用数: 0 h-index: 0机构: Univ Evry, Univ Paris Saclay, INTEGRARE, Genethon,INSERM,UMR951, F-91002 Evry, France Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, SpainBosch, Fatima论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra 08193, Spain Inst Salud Carlos III, Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra 08193, Spain
- [4] Treatment of Infantile-Onset Pompe Disease in a Rat Model with Muscle-Directed AAV Gene TherapyMOLECULAR THERAPY, 2023, 31 (04) : 785 - 785Garcia, Miquel论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainMunoz, Sergio论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainBertolin, Joan论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainJimenez, Veronica论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainJaen, Maria Luisa论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainPujol, Anna论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainVila, Laia论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainSacristan, Victor论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainBarbon, Elena论文数: 0 引用数: 0 h-index: 0机构: INTEGRARE, GENETHON, Evry, France Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainRonzitti, Giuseppe论文数: 0 引用数: 0 h-index: 0机构: INTEGRARE, GENETHON, Evry, France Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainEl Andari, Jihad论文数: 0 引用数: 0 h-index: 0机构: Univ Heidelberg Hosp, Heidelberg, Germany Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainTulalamba, Warut论文数: 0 引用数: 0 h-index: 0机构: Free Univ Brussels VUB, Brussels, Belgium Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainPham, Quang Hong论文数: 0 引用数: 0 h-index: 0机构: Free Univ Brussels VUB, Brusels, Belgium Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainRuberte, Jesus论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Sch Vet Med, Dept Anim Hlth & Anat, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainVandendriessche, Thierry C.论文数: 0 引用数: 0 h-index: 0机构: Free Univ Brussels VUB, Brussels, Belgium Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainChuah, Marinee K. L.论文数: 0 引用数: 0 h-index: 0机构: Free Univ Brussels, VUB, Brussels, Belgium Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, Spain论文数: 引用数: h-index:机构:Mingozzi, Federico论文数: 0 引用数: 0 h-index: 0机构: INTEGRARE, GENETHON, Evry, France Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, SpainBosch, Fatima论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, Spain
- [5] AAV-mediated gene therapy of Pompe diseaseNEUROMUSCULAR DISORDERS, 2005, 15 (9-10) : 713 - 713Ziegler, RJ论文数: 0 引用数: 0 h-index: 0机构: NIH, Bethesda, MD 20892 USABercury, S论文数: 0 引用数: 0 h-index: 0机构: NIH, Bethesda, MD 20892 USAArmentaro, D论文数: 0 引用数: 0 h-index: 0机构: NIH, Bethesda, MD 20892 USARaben, N论文数: 0 引用数: 0 h-index: 0机构: NIH, Bethesda, MD 20892 USACheng, SH论文数: 0 引用数: 0 h-index: 0机构: NIH, Bethesda, MD 20892 USA
- [6] AAV-GAA Gene Therapy Clears Long Chain Length Neuronal Glycogen in a Pompe Disease Rat ModelPHYSIOLOGY, 2024, 39Fuller, David D.论文数: 0 引用数: 0 h-index: 0Rana, Sabhya论文数: 0 引用数: 0 h-index: 0Ribas, Roberto A.论文数: 0 引用数: 0 h-index: 0Shedlock, Cameron J.论文数: 0 引用数: 0 h-index: 0Larson, Reece论文数: 0 引用数: 0 h-index: 0
- [7] Reduction of Autophagic Accumulation in Pompe Disease Mouse Model Following AAV Gene TherapyMOLECULAR THERAPY, 2017, 25 (05) : 100 - 100McCall, Angela L.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Pediat, Gainesville, FL USA Univ Florida, Pediat, Gainesville, FL USAStankov, Sylvia G.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Pediat, Gainesville, FL USA Univ Florida, Pediat, Gainesville, FL USAFalk, Darin J.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Pediat, Gainesville, FL USA Univ Florida, Pediat, Gainesville, FL USAByrne, Barry论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Pediat, Gainesville, FL USA Univ Florida, Pediat, Gainesville, FL USA
- [8] Advancements in AAV-mediated Gene Therapy for Pompe DiseaseJOURNAL OF NEUROMUSCULAR DISEASES, 2020, 7 (01) : 15 - 31Salabarria, S. M.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Pediat, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, 1600 SW Archer Rd, Gainesville, FL 32610 USA Univ Florida, Dept Pediat, Gainesville, FL 32610 USANair, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Pediat, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, 1600 SW Archer Rd, Gainesville, FL 32610 USA Univ Florida, Dept Pediat, Gainesville, FL 32610 USAClement, N.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Pediat, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, 1600 SW Archer Rd, Gainesville, FL 32610 USA Univ Florida, Dept Pediat, Gainesville, FL 32610 USASmith, B. K.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Phys Therapy, Gainesville, FL 32610 USA Univ Florida, Ctr Resp Res & Rehabil, Gainesville, FL 32610 USA Univ Florida, Dept Pediat, Gainesville, FL 32610 USARaben, N.论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Lab Prot Trafficking & Organelle Biol, Cell & Dev Biol Ctr, NIH, Bldg 10, Bethesda, MD 20892 USA Univ Florida, Dept Pediat, Gainesville, FL 32610 USAFuller, D. D.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Phys Therapy, Gainesville, FL 32610 USA Univ Florida, Ctr Resp Res & Rehabil, Gainesville, FL 32610 USA Univ Florida, Dept Pediat, Gainesville, FL 32610 USAByrne, B. J.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Pediat, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, 1600 SW Archer Rd, Gainesville, FL 32610 USA Univ Florida, Dept Pediat, Gainesville, FL 32610 USACorti, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Pediat, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, 1600 SW Archer Rd, Gainesville, FL 32610 USA Univ Florida, Dept Pediat, Gainesville, FL 32610 USA
- [9] Neonatal gene therapy restores breathing in a rat model of Pompe diseasePHYSIOLOGY, 2023, 38Fuller, David论文数: 0 引用数: 0 h-index: 0Rana, Sabhya论文数: 0 引用数: 0 h-index: 0Pope, Megan论文数: 0 引用数: 0 h-index: 0Thakre, Prajwal论文数: 0 引用数: 0 h-index: 0Corti, Manuela论文数: 0 引用数: 0 h-index: 0Byrne, Barry论文数: 0 引用数: 0 h-index: 0
- [10] Tongue and Hypoglossal Motoneuron Gene Therapy in a Rat Model of Pompe DiseaseFASEB JOURNAL, 2021, 35Singer, Michele论文数: 0 引用数: 0 h-index: 0Rana, Sabhya论文数: 0 引用数: 0 h-index: 0Pope, Megan论文数: 0 引用数: 0 h-index: 0Patterson, LiAna论文数: 0 引用数: 0 h-index: 0Corti, Manuela论文数: 0 引用数: 0 h-index: 0Byrne, Barry论文数: 0 引用数: 0 h-index: 0Fuller, David论文数: 0 引用数: 0 h-index: 0