Prevention of photoreceptor cell degeneration in P23H rats after allele-specific knockdown of mutant Rhodopsin RNA expression using antisense oligonucleotide (ASO) treatment

被引：0
|
作者：
Murray, Sue F. [1 ]
Jazayeri, Ali [1 ]
LaVail, Matthew M. [2 ]
Matthes, Michael T. [2 ]
Yasumura, Douglas [2 ]
Yang, Haidong [2 ]
McCaleb, Michael [1 ]
Peralta, Raechel [1 ]
Watt, Andy [1 ]
Monia, Brett [1 ]
机构：
[1] ISIS Pharmaceut, Exploratory Res, Carlsbad, CA 92008 USA
[2] UCSF, Sch Med, San Francisco, CA USA
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2014年 / 55卷 / 13期
关键词：
649 photoreceptors: visual performance; 696 retinal degenerations: hereditary; 702; retinitis;
D O I：
暂无
中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
摘要：
1258
引用
收藏
页数：3
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