Incentivizing Therapies for Rare Diseases

被引:1
|
作者
Karas, Laura [1 ]
机构
[1] Harvard Pilgrim Hlth Care Inst, Dept Populat Med, 401 Pk Dr,Ste 401, Boston, MA 02215 USA
来源
关键词
D O I
10.1001/jama.2019.6954
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:464 / 465
页数:2
相关论文
共 50 条
  • [1] Incentivizing Therapies for Rare Diseases Reply
    Thomas, Shailin
    Caplan, Arthur
    JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION, 2019, 322 (05): : 465 - 465
  • [2] Gene Therapies for Rare Diseases
    不详
    JOURNAL OF NUCLEAR MEDICINE, 2022, 63 (01) : 22N - 22N
  • [3] ADVANCED THERAPIES FOR RARE DISEASES
    Fillat, Cristina
    del Rio, Marcela
    Martinez-Santamaria, Lucia
    Bueren, Juan A.
    ARBOR-CIENCIA PENSAMIENTO Y CULTURA, 2018, 194 (789)
  • [4] Curative gene therapies for rare diseases
    Rocio Maldonado
    Sami Jalil
    Kirmo Wartiovaara
    Journal of Community Genetics, 2021, 12 : 267 - 276
  • [5] Gene therapies for rare neurological diseases
    Burgunder, J.
    EUROPEAN JOURNAL OF NEUROLOGY, 2022, 29 : 41 - 41
  • [6] Curative gene therapies for rare diseases
    Maldonado, Rocio
    Jalil, Sami
    Wartiovaara, Kirmo
    JOURNAL OF COMMUNITY GENETICS, 2021, 12 (02) : 267 - 276
  • [7] Health Technology Assessment and Appraisal of Therapies for Rare Diseases
    Iskrov, Georgi
    Miteva-Katrandzhieva, Tsonka
    Stefanov, Rumen
    RARE DISEASES EPIDEMIOLOGY: UPDATE AND OVERVIEW, 2ND EDITION, 2017, 1031 : 221 - 231
  • [8] Regenerative Medicine for the Youngest: Customized Therapies for Rare Diseases
    De Coppi, Paolo
    EUROPEAN JOURNAL OF PEDIATRIC SURGERY, 2014, 24 (03) : 203 - 204
  • [9] Pathways from Immune Profiling to Therapies for Rare Diseases
    Ma, Averil
    MED, 2021, 2 (01): : 14 - 15
  • [10] Rare Diseases Should we rely on chaperone therapies?
    Crebat, Lea
    ACTUALITES PHARMACEUTIQUES, 2016, 55 (559): : 6 - 6