Efficacy and Safety of Intravenous Efgartigimod 10 Mg/Kg in Adult Patients with Primary Immune Thrombocytopenia: Advance, a Phase 3 Clinical Trial in Progress

被引:0
|
作者
Newland, Adrian C.
Liebman, Howard A.
McDonald, Vickie
Michel, Marc
Miyakawa, Yoshitaka
Parys, Wim
De Haard, Hans
Ulrichts, Peter
Godar, Marie
De Beuf, Kristof
Ayguasanosa, Jaume
Broome, Catherine M.
Kuter, David J.
机构
关键词
D O I
10.1182/blood-2020-141161
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页数:4
相关论文
共 50 条
  • [1] Efficacy and Safety of Intravenous Efgartigimod in Adults with Primary Immune Thrombocytopenia: Results of a Phase 3, Multicenter, Double-Blinded, Placebo-Controlled, Randomized Clinical Trial (ADVANCE IV)
    Broome, Catherine M.
    McDonald, Vickie
    Miyakawa, Yoshitaka
    Carpenedo, Monica
    Kuter, David J.
    Al-Samkari, Hanny
    Bussel, James B.
    Godar, Marie
    Ayguasanosa, Jaume
    De Beuf, Kristof
    Rodeghiero, Francesco
    Michel, Marc
    Newland, Adrian C.
    [J]. BLOOD, 2022, 140
  • [2] Intravenous efgartigimod in adults with primary immune thrombocytopenia: Results from the ADVANCE IV trial
    Mcdonald, Vickie
    Broome, Catherine M.
    Miyakawa, Yoshitaka
    Carpenedo, Monica
    Kuter, David J.
    Carpenedo, Monica
    Kuter, David J.
    Al-Samkari, Hanny
    Bussel, James B.
    Godar, Marie
    Ayguasanosa, Jaume
    De Beuf, Kristof
    Rodeghiero, Francesco
    Michel, Marc
    Newland, Adrian
    [J]. BRITISH JOURNAL OF HAEMATOLOGY, 2023, 201 : 23 - 23
  • [3] Efficacy and safety of the neonatal Fc receptor inhibitor efgartigimod in adults with primary immune thrombocytopenia (ADVANCE IV): a multicentre, randomised, placebo-controlled, phase 3 trial
    Broome, Catherine M.
    McDonald, Vickie
    Miyakawa, Yoshitaka
    Carpenedo, Monica
    Kuter, David J.
    Al-Samkari, Hanny
    Bussel, James B.
    Godar, Marie
    Ayguasanosa, Jaume
    De Beuf, Kristof
    Rodeghiero, Francesco
    Michel, Marc
    Newland, Adrian
    [J]. LANCET, 2023, 402 (10413): : 1648 - 1659
  • [4] Efficacy and Safety of a New 10% Intravenous Immunoglobulin Product in Patients with Primary Immune Thrombocytopenia (ITP)
    Hong, Junshik
    Bang, Soo-Mee
    Mun, Yeung-Chul
    Yhim, Ho-Young
    Lee, Jaehoon
    Lim, Hyeong-Seok
    Oh, Doyeun
    [J]. JOURNAL OF KOREAN MEDICAL SCIENCE, 2018, 33 (19)
  • [5] Phase 2 Study of Efgartigimod, a Novel FcRn Antagonist, in Adult Patients with Primary Immune Thrombocytopenia
    Newland, Adrian C.
    Sanchez-Gonzalez, Blanca
    Rejto, Laszlo
    Egyed, Miklos
    Romanyuk, Nataliya
    Godar, Marie
    Verschueren, Katrien
    Gandini, Domenica
    Ulrichts, Peter
    Beauchamp, Jon
    Dreier, Torsten
    Ward, E. Sally
    Michel, Marc
    Liebman, Howard A.
    De Haard, Hans
    Leupin, Nicolas
    Kuter, David J.
    [J]. BLOOD, 2019, 134
  • [6] Phase 2 study of efgartigimod, a novel FcRn antagonist, in adult patients with primary immune thrombocytopenia
    Newland, Adrian C.
    Sanchez-Gonzalez, Blanca
    Rejto, Laszlo
    Egyed, Miklos
    Romanyuk, Nataliya
    Godar, Marie
    Verschueren, Katrien
    Gandini, Domenica
    Ulrichts, Peter
    Beauchamp, Jon
    Dreier, Torsten
    Ward, E. Sally
    Michel, Marc
    Liebman, Howard A.
    de Haard, Hans
    Leupin, Nicolas
    Kuter, David J.
    [J]. AMERICAN JOURNAL OF HEMATOLOGY, 2020, 95 (02) : 178 - 187
  • [7] Pharmacokinetic/Pharmacodynamic Simulations Guide Selection of the Dose for Administration of Efgartigimod Subcutaneously in a Phase 3 Clinical Trial in Patients with Primary Immune Thrombocytopenia
    Wittlin, Beatriz
    McDonald, Vickie
    Ghanima, Waleed
    Broome, Catherine
    Hultberg, Anna
    Gandini, Domenica
    Parys, Wim
    Hofman, Erik
    Miyakawa, Yoshitaka
    Jain, Shivi
    Carpenedo, Monica
    Oliva, Esther
    [J]. BRITISH JOURNAL OF HAEMATOLOGY, 2022, 197 : 44 - 44
  • [8] Efficacy and safety of BT595 (10% human intravenous immunoglobulin) in adult patients with chronic immune thrombocytopenia
    Demeter, Judit
    Hamed, Aryan
    Laszlo, Szerafin
    Suvajdzic, Nada
    Aigner, Silke
    Boerner, Birgit
    Staiger, Christiane
    [J]. TRANSFUSION MEDICINE, 2023, 33 (02) : 165 - 173
  • [9] Efficacy and Safety of IQYMUNE (R), a Ten Percent Intravenous Immunoglobulin in Adult Patients With Chronic, Primary Immune Thrombocytopenia
    Rodeghiero, Francesco
    Woszczyk, Dariusz
    Slama, Borhane
    Melikyan, Anait
    Viallard, Jean-Francois
    Ouaja, Rabye
    Cisse, Ousmane Alfa
    Sadoun, Alain
    Salama, Abdulgabar
    [J]. JOURNAL OF HEMATOLOGY, 2018, 7 (03) : 87 - 95
  • [10] Efficacy and safety of a new intravenous immunoglobulin 10% formulation (octagam® 10%) in patients with immune thrombocytopenia
    Robak, Tadeusz
    Mainau, Claudia
    Pyringer, Barbara
    Chojnowski, Krzysztof
    Warzocha, Krzysztof
    Dmoszynska, Anna
    Straub, Jan
    Imbach, Paul
    [J]. HEMATOLOGY, 2010, 15 (05) : 351 - 359