Tyrosine chemically modified AAV capsids to achieve ever more efficient retinal transduction

被引:0
|
作者
Varin, J. [1 ]
Demilly, J. [1 ]
Bouzelha, M. [1 ]
Pavageau, K. [1 ]
Alvarez-Dorta, D. [1 ]
Ducloyer, J. B. [1 ,2 ]
Mellet, A. [1 ]
Adjali, O. [1 ]
Deniaud, D. [1 ]
Cronin, T. [1 ]
Mevel, M. [1 ]
机构
[1] Univ Nantes, Nantes, France
[2] CHU Nantes, Nantes, France
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
P025
引用
收藏
页码:A32 / A32
页数:1
相关论文
共 21 条
  • [1] Engineered AAV Capsids for Efficient Muscle Transduction in NHP
    Chen, Shuyuan
    Wu, Zhenhua
    Pang, Xiaodong
    Li, Shaoyong
    Li, Zhongwan
    Zhang, Runyuan
    Li, Guanlin
    Lan, Xing
    Jiang, Yuling
    Zheng, Yanyan
    Wan, Changpeng
    Ye, Guo-jie
    MOLECULAR THERAPY, 2024, 32 (04) : 267 - 267
  • [2] In Vivo Quantification Of Photoreceptor Transduction Efficiency Using Novel Modified AAV Capsids
    Ryals, Renee
    Kay, Christine
    Boye, Sanford
    Min, Seok-Hong
    Ayala, Andrea
    Hauswirth, William
    Boye, Shannon
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2013, 54 (15)
  • [3] AI-Aided AAV Capsids Design for Efficient Retina Transduction in NHP
    Chen, Shuyuan
    Pang, Xiaodong
    Wan, Changpeng
    Li, Zhongwan
    Wu, Weiwei
    Zhang, Runyuan
    Lan, Xing
    Li, Guanlin
    Wu, Zhenhua
    Li, Shaoyong
    Ye, Guo-jie
    MOLECULAR THERAPY, 2024, 32 (04) : 682 - 682
  • [4] Tyrosine Chemically Modified AAV Vectors for Gene Delivery in Retina
    Mevel, Mathieu
    Leray, Aurelien
    Bouzelha, Mohammed
    Gouin, Sebastien
    Demilly, Joanna
    Penaud-Budloo, Magalie
    Adjali, Oumeya
    Ayuso, Eduard
    Deniaud, David
    Cronin, Therese
    MOLECULAR THERAPY, 2021, 29 (04) : 140 - 140
  • [5] Efficient Transduction in Kidney Tubules with Minimum Off-Target Effects by Renal Vein Injection of Select AAV Capsids
    Furusho, Taisuke
    Adachi, Kei
    Galbraith-Liss, Mia
    Sairavi, Anusha
    Das, Ranjan
    Nakai, Hiroyuki
    MOLECULAR THERAPY, 2023, 31 (04) : 232 - 232
  • [6] An approach to identify novel Adeno-Associated Virus (AAV) capsids that provide enhanced retinal cell transduction following intravitreal injections
    Powers, John Michael
    Adachi, Kei
    Sivyer, Benjamin
    Taylor, William Rowland
    Pennesi, Mark E.
    Nakai, Hiroyuki
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2016, 57 (12)
  • [7] A modified AAV2/6 enhances retinal microglial transduction in a layer-specific manner
    Maes, Margaret
    Woegenstein, Gabriele
    Colombo, Gloria
    Siegert, Sandra
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2021, 62 (08)
  • [8] A novel modified deep intravitreal injection improves Adeno-associated virus (AAV)-mediated retinal transduction
    Park, T.
    Madrakhimov, S. B.
    Yang, J.
    Ahn, D.
    Ha, T.
    HUMAN GENE THERAPY, 2019, 30 (11) : A113 - A113
  • [9] Efficient Retinal Transduction by AAV Variants Identified via Directed Evolution and Screening in Non-Human Primate
    Boye, Shannon E.
    Choudhury, Shreyasi
    Marsic, Damien
    Kondratov, Oleksandr
    Potter, Mark
    Peterson, James
    Calabro, Kaitlyn
    Strang, Christianne
    Zolotukhin, Sergei
    Gamlin, Paul
    Boye, Sanford
    MOLECULAR THERAPY, 2020, 28 (04) : 257 - 258
  • [10] Sustained and Efficient Transduction of Retinal Pigment Epithelial Cells by Nanoparticles Containing Modified Vectors
    Koirala, A.
    Han, Z.
    Makkia, R. S.
    Cooper, M. J.
    Naash, M. I.
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2010, 51 (13)