GROWTH PATTERNS OF 14 PATIENTS WITH MUCOPOLYSACCHARIDOSIS I: RETROSPECTIVE ANALYSIS AND EFFICACY OF RECOMBINANT HUMAN α-L-IDURONIDASE (LARONIDASE)

被引：0
|
作者：
Jurecka, A. [1 ]
Rozdzynska, A. [2 ]
Marucha, J. [3 ]
Czartoryska, B. [4 ]
Tylki-Szymanska, A. [1 ]
机构：
[1] Childrens Mem Hlth Inst, Dept Metab Dis Endocrinol & Diabetol, Warsaw, Woj Mazowieckie, Poland
[2] Childrens Mem Hlth Inst, Anthropometry Lab, Warsaw, Woj Mazowieckie, Poland
[3] Childrens Mem Hlth Inst, Dept Phys Therapy, Warsaw, Woj Mazowieckie, Poland
[4] Inst Psychiat & Neurol, Dept Genet, Warsaw, Woj Mazowieckie, Poland
来源：
MOLECULAR GENETICS AND METABOLISM | 2009年 / 98卷 / 1-2期
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D O I：
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中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
357
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收藏
页码：62 / 62
页数：1
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