AAV9 intracerebroventricular gene therapy improves lifespan and normalises long-term locomotor behaviour in a mouse model of Niemann-Pick type C1 disease

被引：0

作者：

Hughes, Michael ^{[1
]}

Smith, Dave ^{[2
]}

Morris, Lauren ^{[2
]}

Fletcher, Claire ^{[2
]}

Colaco, Allie ^{[2
]}

Huebecker, Mylene ^{[2
]}

Massaro, Giulia ^{[1
]}

Tordo, Julie ^{[3
]}

Palomar, Nuria ^{[3
]}

Henckaerts, Els ^{[3
]}

Waddington, Simon ^{[4
]}

Platt, Fran ^{[2
]}

Rahim, Ahad ^{[1
]}

机构：

[1] UCL Sch Pharm, London, England

[2] Univ Oxford, Oxford, England

[3] Kings Coll London, London, England

[4] UCL Inst Womens Hlth, London, England

来源：

HUMAN GENE THERAPY | 2018年 / 29卷 / 07期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

PO09

引用

页码：A8 / A8

页数：1

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