EXPRESSION, BIOACTIVITY, AND SAFETY 1 YEAR AFTER ADENO-ASSOCIATED VIRAL VECTOR TYPE 2-MEDIATED DELIVERY OF NEURTURIN TO THE MONKEY NIGROSTRIATAL SYSTEM SUPPORT CERE-120 FOR PARKINSON'S DISEASE COMMENTS

被引:0
|
作者
Franz, Colin K.
Starr, Philip A.
机构
关键词
D O I
暂无
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
引用
收藏
页码:612 / 613
页数:2
相关论文
共 5 条
  • [1] EXPRESSION, BIOACTIVITY, AND SAFETY 1 YEAR AFTER ADENO-ASSOCIATED VIRAL VECTOR TYPE 2-MEDIATED DELIVERY OF NEURTURIN TO THE MONKEY NIGROSTRIATAL SYSTEM SUPPORT CERE-120 FOR PARKINSON'S DISEASE
    Herzo, Christopher D.
    Brown, Lamar
    Gammon, Dawn
    Kruegel, Brian
    Lin, Richard
    Wilson, Alistair
    Bolton, Ariadne
    Printz, Marie
    Gasmi, Mehdi
    Bishop, Kathie M.
    Kordower, Jeffrey H.
    Bartus, Raymond T.
    NEUROSURGERY, 2009, 64 (04) : 602 - 612
  • [2] AAV2 - mediated delivery of human neurturin to the rat nigrostriatal system: Long-term efficacy and tolerability of CERE-120 for Parkinson's disease
    Gasmi, Mehdi
    Brandon, Eugene P.
    Herzoga, Christopher D.
    Wilson, Alistair
    Bishop, Kathie M.
    Hofer, Eva K.
    Cunningham, Justine J.
    Printz, Marie A.
    Kordower, Jeffrey H.
    Bartus, Raymond T.
    NEUROBIOLOGY OF DISEASE, 2007, 27 (01) : 67 - 76
  • [3] Safety and tolerability of intraputaminal delivery of CERE-120 (adeno-associated virus serotype 2-neurturin) to patients with idiopathic Parkinson's disease: an open-label, phase I trial
    Marks, William J., Jr.
    Ostrem, Jill L.
    Verhagen, Leonard
    Starr, Philip A.
    Larson, Paul S.
    Bakay, Roy A. E.
    Taylor, Robin
    Cahn-Weiner, Deborah A.
    Stoessl, A. Jon
    Olanow, C. Warren
    Bartus, Raymond T.
    LANCET NEUROLOGY, 2008, 7 (05): : 400 - 408
  • [4] Phase I study of putaminal gene transfer with adeno-associated virus serotype 2 [AAV2]-neurturin [NTN] (CERE-120) for Parkinson's disease: Preliminary observations
    Marks, WJ
    Metman, LAV
    Starr, PA
    Larson, PS
    Bakay, RA
    Taylor, R
    Cahn-Weiner, D
    Bartus, RT
    Ostrem, JL
    NEUROLOGY, 2006, 66 (05) : A185 - A185
  • [5] Adeno-Associated Virus Type 2 Vector-Mediated Glial Cell Line-Derived Neurotrophic Factor Gene Transfer Induces Neuroprotection and Neuroregeneration in a Ubiquitin-Proteasome System Impairment Animal Model of Parkinson's Disease
    Du, Yunlan
    Zhang, Xiaojie
    Tao, Qingqing
    Chen, Sheng
    Le, Weidong
    NEURODEGENERATIVE DISEASES, 2013, 11 (03) : 113 - 128