Assessment of Toxicity and Biodistribution of an AAV2/8 Vector-Mediated Immunomodulatory Gene Therapy in Mice With Pompe Disease

被引：0
|
作者：
Han, Sang-oh [1 ]
Wang, Gensheng [2 ]
Young, Sarah [1 ]
Bali, Deeksha [1 ]
Benson, Janet [2 ]
Koeberl, Dwight [1 ]
机构：
[1] Duke Univ, Med Ctr, Dept Pediat, Div Med Genet, Durham, NC 27710 USA
[2] Lovelace Resp Res Inst, Appl Toxicol & Gene Therapy Pharm Tox Program, Albuquerque, NM USA
来源：
MOLECULAR THERAPY | 2014年 / 22卷
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
47
引用
收藏
页码：S19 / S19
页数：1
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