Modelling Machado-Joseph Disease in patientderived isogenic lines by CRISPR/Cas9-mediated correction of ATXN3-CAG expansion

被引：0
|
作者：
Perdigao, P. [1 ,2 ]
Matos, C. [1 ,2 ]
Lopes, S. [1 ,2 ]
Fernandes, R. [1 ,2 ,3 ]
Lopes, M. [1 ,2 ,3 ,4 ]
Conceicao, A. [1 ,2 ]
Faro, R. [1 ,2 ]
Santana, M. [1 ,2 ]
Adao, D. [1 ,2 ]
Rufino-Ramos, D. [1 ,2 ,3 ]
Leandro, K. [1 ,2 ,3 ]
Nobre, R. [1 ,2 ,4 ]
de Almeida, L. Pereira [1 ,2 ,5 ]
机构：
[1] Univ Coimbra, CNC Ctr Neurosci & Cell Biol, Coimbra, Portugal
[2] Univ Coimbra, CIBB Ctr Innovat Biomed & Biotechnol, Coimbra, Portugal
[3] Univ Coimbra, Inst Interdisciplinary Res, Coimbra, Portugal
[4] Univ Coimbra, ViraVector, Viral Vector Gene Transfer Core Facil, Coimbra, Portugal
[5] Univ Coimbra, Fac Pharm, Coimbra, Portugal
来源：
HUMAN GENE THERAPY | 2022年 / 33卷 / 23-24期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P356
引用
收藏
页码：A119 / A119
页数：1
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