β-Globin Gene Editing in Human Cells Using TALENs and ssDNA Oligonucleotides: Towards a Gene Repair Approach for Sickle Cell Anemia and β-Thalassemias

被引：0
|
作者：
Mansilla-Soto, Jorge [1 ]
Socci, Nicholas [2 ]
Leifman, Yan [1 ]
Sadelain, Michel [1 ]
机构：
[1] Mem Sloan Kettering Canc Ctr, Ctr Cell Engn, New York, NY 10021 USA
[2] Mem Sloan Kettering Canc Ctr, Bioinformat Core Facil, New York, NY 10021 USA
来源：
MOLECULAR THERAPY | 2014年 / 22卷
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
557
引用
收藏
页码：S216 / S216
页数：1
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