Vestronidase Alfa: A Review in Mucopolysaccharidosis VII (vol 33, pg 233, 2019)

被引：0
|
作者：
McCafferty, Emma H. [1 ]
Scott, Lesley J. [1 ]
机构：
[1] Springer, Private Bag 65901, Auckland 0754, New Zealand
来源：
BIODRUGS | 2019年 / 33卷 / 03期
关键词：
D O I：
10.1007/s40259-019-00353-6
中图分类号：
R73 [肿瘤学];
学科分类号：
100214 ;
摘要：
The article Vestronidase Alfa: A Review in Mucopolysaccharidosis VII, written by Emma H. McCafferty and Lesley J. Scott, was originally published Online First without open access.
引用
收藏
页码：343 / 343
页数：1
相关论文
共 50 条
  • [1] Vestronidase Alfa: A Review in Mucopolysaccharidosis VII
    McCafferty, Emma H.
    Scott, Lesley J.
    [J]. BIODRUGS, 2019, 33 (02) : 233 - 240
  • [2] Vestronidase Alfa: A Review in Mucopolysaccharidosis VII
    Emma H. McCafferty
    Lesley J. Scott
    [J]. BioDrugs, 2019, 33 : 233 - 240
  • [3] Correction to: Vestronidase Alfa: A Review in Mucopolysaccharidosis VII
    Emma H. McCafferty
    Lesley J. Scott
    [J]. BioDrugs, 2019, 33 : 343 - 343
  • [4] Early clinical response and continued safety with vestronidase ALFA for the treatment of mucopolysaccharidosis VII (MPS VII)
    Burton, Barbara
    Giugliani, Roberto
    Gonzalez-Meneses, Antonio
    Grant, Christina Lee
    Scarpa, Maurizio
    Sun, Angela
    Wang, Raymond
    Van der Ploeg, Ans
    Martins, Esmeralda
    Durand, Consuelo
    Chabrol, Brigitte
    Hetzer, Joel
    Malkus, Betsy
    Cohen, Jeanne
    Marsden, Deborah
    Merritt, J. Lawrence, II
    [J]. MOLECULAR GENETICS AND METABOLISM, 2024, 141 (04)
  • [5] Open-label phase 1/2 study of vestronidase alfa for mucopolysaccharidosis VII
    Jones, Simon
    Coker, Mahmut
    Gonzalez-Meneses Lopez, Antonio
    Sniadecki, Jennifer
    Mayhew, Jill
    Hensman, Pauline
    Jurecka, Agnieszka
    [J]. MOLECULAR GENETICS AND METABOLISM REPORTS, 2021, 28
  • [6] The long-term safety and efficacy of vestronidase alfa, rhGUS enzyme replacement therapy, in subjects with mucopolysaccharidosis VII (vol 129, pg 219, 2020)
    Wang, Raymond Y.
    da Silva Franco, Jose Francisco
    Lopez-Valdez, Jaime
    Martins, Esmeralda
    Sutton, Vernon Reid
    Whitley, Chester B.
    Zhang, Lin
    Cimms, Tricia
    Marsden, Deborah
    Jurecka, Agnieszka
    Harmatz, Paul
    [J]. MOLECULAR GENETICS AND METABOLISM, 2020, 131 (1-2) : 285 - 285
  • [7] VESTRONIDASE ALFA FOR THE TREATMENT OF MUCOPOLYSACCHARIDOSIS VII (MPS VII): UPDATED RESULTS FROM A NOVEL, LONGITUDINAL, MULTICENTER DISEASE MONITORING PROGRAM
    Giugliani, Roberto
    Gonzalez-Meneses, Antonio
    Grant, Christina Lee
    Scarpa, Maurizio
    Sun, Angela
    Wang, Raymond
    Hetzer, Joel
    Marsden, Deborah
    Merritt, J. Lawrence, II
    [J]. MOLECULAR GENETICS AND METABOLISM, 2023, 138 (03) : 50 - 51
  • [8] Vestronidase alfa for the treatment of Mucopolysaccharidosis VII (MPS VII): Updated results from a novel, longitudinal, multicenter disease monitoring program
    Guigliani, Roberto
    Lopez, Antonio Gonzalez-Meneses
    Scarpa, Maurizio
    Lau, Heather
    Zhang, Lin
    Malkus, Betsy
    Marsden, Deborah
    Merritt, J. Lawrence, II
    [J]. GENETICS IN MEDICINE, 2022, 24 (03) : S101 - S101
  • [9] The long-term safety and efficacy of vestronidase alfa, rhGUS enzyme replacement therapy, in subjects with mucopolysaccharidosis VII
    Wang, Raymond Y.
    da Silva Franco, Jose Francisco
    Lopez-Valdez, Jaime
    Martins, Esmeralda
    Sutton, Vernon Reid
    Whitley, Chester B.
    Zhang, Lin
    Cimms, Tricia
    Marsden, Deborah
    Jurecka, Agnieszka
    Harmatz, Paul
    [J]. MOLECULAR GENETICS AND METABOLISM, 2020, 129 (03) : 219 - 227
  • [10] UPDATED RESULTS FROM A NOVEL, LONGITUDINAL, MULTICENTER DISEASE MONITORING PROGRAM (DMP) OF VESTRONIDASE ALFA FOR THE TREATMENT OF MUCOPOLYSACCHARIDOSIS VII (MPS VII)
    Giugliani, Roberto
    Gonzalez-Meneses, Antonio
    Scarpa, Maurizio
    Lau, Heather
    Zhang, Lin
    Malkus, Betsy
    Marsden, Deborah
    Merritt, J. Lawrence, II
    [J]. MOLECULAR GENETICS AND METABOLISM, 2022, 135 (04) : 273 - 274
12345