Correction of Visual and Auditory Function by AAV9-Mediated Gene Therapy in a Mouse Model of Mucopolysaccharidosis Type IIIB

被引：0
|
作者：
Ribera, Albert [1 ]
Motas, Sandra [1 ]
Ramirez, Laura [2 ]
Marco, Sara [1 ]
Sanchez, Victor [1 ]
Sanchez, Xavier [1 ]
Bertolin, Joan [1 ]
Perez, Jennifer A. [1 ]
Leon, Xavier [1 ]
Varela-Nieto, Isablel [3 ]
de la Villa, Pedro [2 ]
Haurigot, Virginia [1 ]
Bosch, Fatima [1 ]
机构：
[1] Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra, Spain
[2] Univ Alcala De Henares, Dept Syst Biol, Alcala De Henares, Spain
[3] Univ Autonoma Madrid, CSIC, Alberto Sols Biomed Res Inst, Madrid, Spain
来源：
MOLECULAR THERAPY | 2018年 / 26卷 / 05期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
241
引用
收藏
页码：114 / 114
页数：1
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