Number Needed to Treat (NNT) in Spinal Muscular Atrophy Type 1 (SMA1) with AVXS-101 Relative to Nusinersen

被引：0
|
作者：
Droege, Marcus [1 ]
Dabbous, Omar [1 ]
Cloutier, Martin [2 ]
Guerin, Annie [2 ]
Pivneva, Irina [2 ]
Wu, Eric Q. [2 ]
Sproule, Douglas M. [1 ]
机构：
[1] AveXis Inc, Bannockburn, IL USA
[2] Anal Grp Inc, Boston, MA USA
来源：
NEUROLOGY | 2019年 / 92卷 / 15期
关键词：
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
P1.6-056
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页数：2
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