[1] Wellcome Trust Sanger Inst, Cambridge, England
[2] Cambridge Univ Hosp NHS Fdn Trust, Dept Paediat, Cambridge, England
[3] Ist Giannina Gaslini IRCCS, Lab Cellule Staminali & Terapie Cellulari, Genoa, Italy
[4] Univ Turin, Dept Clin & Biol Sci, Turin, Italy
[5] Inst Biomed & Biotecnol Cantabria, Cantabria, Spain
[6] Univ Cambridge, Dept Haematol, Cambridge, England
[7] Cambridge Univ Hosp NHS Fdn Trust, Dept Haematol, Cambridge, England