SAFETY AND EFFICACY OF LUMACAFTOR/IVACAFTOR IN PEDIATRIC CYSTIC FIBROSIS PATIENTS

被引:0
|
作者
Wainwright, C. [1 ]
Chilvers, M. [2 ]
Hug, C. [3 ]
Marigowda, G. [3 ]
Tian, S. [3 ]
Solomon, M. [4 ]
Black, P. [5 ]
Rosenfeld, M. [6 ]
Sawicki, G. [7 ]
Hoppe, J. [8 ]
机构
[1] Lady Cilento Childrens Hosp, South Brisbane, Australia
[2] British Columbia Childrens Hosp, Vancouver, BC, Canada
[3] Vertex Pharmaceut Inc, Boston, MA USA
[4] Hosp Sick Children, Toronto, ON, Canada
[5] Childrens Mercy Hosp, Kansas City, MO 64108 USA
[6] Univ Washington, Sch Med, Seattle Childrens Hosp, Seattle, WA 98195 USA
[7] Harvard Med Sch, Boston, MA USA
[8] Univ Colorado, Sch Med, Childrens Hosp Colorado, Boulder, CO 80309 USA
关键词
D O I
暂无
中图分类号
R56 [呼吸系及胸部疾病];
学科分类号
摘要
TP 068
引用
收藏
页码:141 / 141
页数:1
相关论文
共 50 条
  • [1] Safety and efficacy of treatment with lumacaftor in combination with ivacaftor in younger patients with cystic fibrosis
    Cheng, Pi Chun
    Alexiou, Stamatia
    Rubenstein, Ronald C.
    EXPERT REVIEW OF RESPIRATORY MEDICINE, 2019, 13 (05) : 417 - 423
  • [2] The safety of lumacaftor and ivacaftor for the treatment of cystic fibrosis
    Guevara, Maria Talamo
    McColley, Susanna A.
    EXPERT OPINION ON DRUG SAFETY, 2017, 16 (11) : 1305 - 1311
  • [3] Lumacaftor/Ivacaftor (Orkambi) for Cystic Fibrosis
    不详
    MEDICAL LETTER ON DRUGS AND THERAPEUTICS, 2016, 58 (1491): : 41 - 42
  • [4] Pathogen acquisition in patients with cystic fibrosis receiving ivacaftor or lumacaftor/ivacaftor
    Singh, Sachinkumar B.
    McLearn-Montz, Amanda J.
    Milavetz, Francesca
    Gates, Levi K.
    Fox, Christopher
    Murry, Logan T.
    Sabus, Ashley
    Porterfield, Harry S.
    Fischer, Anthony J.
    PEDIATRIC PULMONOLOGY, 2019, 54 (08) : 1200 - 1208
  • [5] Lumacaftor/Ivacaftor: A Review in Cystic Fibrosis
    Emma D. Deeks
    Drugs, 2016, 76 : 1191 - 1201
  • [6] Lumacaftor/Ivacaftor: A Review in Cystic Fibrosis
    Deeks, Emma D.
    DRUGS, 2016, 76 (12) : 1191 - 1201
  • [7] PHARMACOKINETIC INTERACTION BETWEEN IVACAFTOR AND LUMACAFTOR IN CYSTIC FIBROSIS PATIENTS
    Hanafin, P.
    Rao, G.
    Schneider-Futschik, E.
    RESPIROLOGY, 2020, 25 : 58 - 58
  • [8] Real-Life Safety and Effectiveness of Lumacaftor-Ivacaftor in Patients with Cystic Fibrosis
    Burgel, Pierre-Regis
    Munck, Anne
    Durieu, Isabelle
    Chiron, Raphael
    Mely, Laurent
    Prevotat, Anne
    Murris-Espin, Marlene
    Porzio, Michele
    Abely, Michel
    Reix, Philippe
    Marguet, Christophe
    Macey, Julie
    Sermet-Gaudelus, Isabelle
    Corvol, Harriet
    Bui, Stephanie
    Lemonnier, Lydie
    Dehillotte, Clemence
    Da Silva, Jennifer
    Paillasseur, Jean-Louis
    Hubert, Dominique
    Mounard, Julie
    Poulet, Claire
    Rames, Cinthia
    Person, Christine
    Troussier, Francoise
    Urban, Thierry
    Dalphin, Marie-Laure
    Dalphin, Jean-Claude
    Pernet, Didier
    Richaud-Thiriez, Benedicte
    Fayon, Mickael
    Macey-Caro, Julie
    Campbell, Karine
    Laurans, Muriel
    Borderon, Corinne
    Heraud, Marie-Christine
    Labbe, Andre
    Montcouquiol, Sylvie
    Bassinet, Laurence
    Remus, Natascha
    Fanton, Annlyse
    Houzel-Charavel, Anne
    Huet, Frederic
    Perez-Martin, Stephanie
    Boldron-Ghaddar, Amale
    Scalbert, Manuela
    Camara, Boubou
    Llerena, Catherine
    Pin, Isabelle
    Quetant, Sebastien
    AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE, 2020, 201 (02) : 188 - 197
  • [9] Pregnancy in two patients with cystic fibrosis treated with lumacaftor/ivacaftor
    Kessler, Christina
    Duebbers, Angelika
    Grosse-Onnebrink, Joerg
    Omran, Heymut
    EUROPEAN RESPIRATORY JOURNAL, 2019, 54
  • [10] EFFECT OF LUMACAFTOR/IVACAFTOR ON EXERCISE CAPACITY IN PATIENTS WITH CYSTIC FIBROSIS
    Tucker, M. A.
    Seigler, N.
    Rodriguez, Miguelez P.
    McKie, K. T.
    Forseen, C.
    Crandall, R. H.
    Harris, R. A.
    PEDIATRIC PULMONOLOGY, 2017, 52 : S393 - S393