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- [1] AsCas12a Gene Editing of HBG1/2 Promoters with EDIT-301 Results in Rapid and Sustained Normalization of Hemoglobin and Increased Fetal Hemoglobin in Patients with Severe Sickle Cell Disease and Transfusion-Dependent Beta-ThalassemiaBLOOD, 2023, 142Hanna, Rabi论文数: 0 引用数: 0 h-index: 0机构: Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USA Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USAFrangoul, Haydar论文数: 0 引用数: 0 h-index: 0机构: Tristar Childrens Hosp, Sarah Cannon Res Inst, Childrens Hosp, Nashville, TN USA Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USAMcKinney, Christopher论文数: 0 引用数: 0 h-index: 0机构: Univ Colorado Anschutz Med Campus, Childrens Hosp Colorado, Aurora, CO USA Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USAPineiro, Luis论文数: 0 引用数: 0 h-index: 0机构: Baylor Univ, Blood & Marrow Transplant Program, Med Ctr, Dallas, TX USA Baylor Univ, Marrow Proc Lab, Med Ctr, Dallas, TX USA Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USAMapara, Markus论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Div Hematol & Oncol, Blood & Marrow Stem Cell Transplantat Program, Irving Med Ctr, New York, NY USA Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USADalal, Jignesh论文数: 0 引用数: 0 h-index: 0机构: Rainbow Babies & Childrens Hosp, Div Hematol & Bone Marrow Transplant, Cleveland, OH USA Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USAChang, Kai-Hsin论文数: 0 引用数: 0 h-index: 0机构: Editas Med Inc, Cambridge, MA USA Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USAJaskolka, Michael论文数: 0 引用数: 0 h-index: 0机构: Editas Med Inc, Cambridge, MA USA Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USAKim, Keunpyo论文数: 0 引用数: 0 h-index: 0机构: Editas Med Inc, Cambridge, MA USA Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USAFarrington, Daphne L.论文数: 0 引用数: 0 h-index: 0机构: Editas Med Inc, Cambridge, MA USA Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USAWally, Maha论文数: 0 引用数: 0 h-index: 0机构: Editas Med Inc, Cambridge, MA USA Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USAMei, Baisong论文数: 0 引用数: 0 h-index: 0机构: Editas Med Inc, Cambridge, MA USA Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USALawal, Adebayo论文数: 0 引用数: 0 h-index: 0机构: Editas Med Inc, Cambridge, MA USA Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USAAfonja, Olubunmi O.论文数: 0 引用数: 0 h-index: 0机构: Editas Med Inc, Cambridge, MA USA Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USAWalters, Mark C.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Benioff Childrens Hosp, Oakland, CA USA Cleveland Clin, Dept Pediat Hematol Oncol & Blood & Marrow Transp, Cleveland, OH USA