Challenges of clinical trial design for DMD

被引：11
|
作者：
Ricotti, Valeria [1 ,2 ]
Muntoni, Francesco [1 ,2 ]
Voit, Thomas [2 ,3 ]
机构：
[1] UCL, Dubowitz Neuromuscular Ctr, Inst Child Hlth, London WC1N 1EH, England
[2] Great Ormond St Hosp Sick Children, London, England
[3] UCL, NIHR Biomed Res Ctr, Inst Child Hlth, London WC1N 1EH, England
来源：
NEUROMUSCULAR DISORDERS | 2015年 / 25卷 / 12期
关键词：
DUCHENNE MUSCULAR-DYSTROPHY; DISEASE PROGRESSION; NATURAL-HISTORY; QUANTIFICATION; GLUCOCORTICOIDS; BOYS; PERINDOPRIL; RESTORATION; AMBULATION; BIOMARKERS;
D O I：
10.1016/j.nmd.2015.10.007
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
[No abstract available]
引用
收藏
页码：932 / 935
页数：4
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