Prevention of Cardiac Disease Features Observed in a Conditional Knockout Mouse Model of Friedreich's Ataxia Treated with a Novel AAV FXN Gene Therapy (AVB-202)

被引：0
|
作者：
Perez, Barbara [1 ]
Wheeler, Jennifer [2 ]
Deiulio, Alex [1 ]
Wright, Christopher I. [1 ]
Byrne, Barry J. [3 ]
Corti, Manuela [3 ]
Pavlath, Grace K. [1 ]
机构：
[1] AavantiBio, Cambridge, MA USA
[2] Aclairo Pharmaceut Dev Grp Inc, Vienna, VA USA
[3] Univ Florida, Gainesville, FL USA
来源：
MOLECULAR THERAPY | 2022年 / 30卷 / 04期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
920
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收藏
页码：434 / 435
页数：2
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