Assessment of Safety and Biodistribution of a miniMECP2 AAV9 Vector for Gene-replacement Therapy of Rett Syndrome in Non-human Primates (NHPs)

被引：0
|
作者：
Prasad, S. [1 ]
Flora, G. [1 ]
Newman, M. [1 ]
Gray, S. J. [2 ]
Sinnett, S. [2 ]
Sadhu, C. [1 ]
机构：
[1] Taysha Gene Therapies R&D, Dept Res & Dev, Dallas, TX USA
[2] Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USA
来源：
HUMAN GENE THERAPY | 2022年 / 33卷 / 23-24期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P238
引用
收藏
页码：A89 / A90
页数：2
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