Simultaneous Disruption of the Erythroid Enhancer of BCL11a and of a BCL11a-Binding Site in the Beta Globin Locus Synergistically Increases Endogenous Fetal Hemoglobin Expression

被引：0
|
作者：
Psatha, Nikoletta [1 ]
Li, Chang [1 ]
Sova, Pavel [1 ]
Liu, Li [1 ]
Wang, Hongjie [1 ]
Papayannopoulou, Thalia [1 ]
Lieber, Andre [1 ]
机构：
[1] Univ Washington, Seattle, WA 98195 USA
来源：
MOLECULAR THERAPY | 2018年 / 26卷 / 05期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
502
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页码：235 / 235
页数：1
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