Outcome measures for Duchenne muscular dystrophy from ambulant to non-ambulant: Implications for clinical trials

被引：0

作者：

Ricotti, V. ^{[1
]}

Eagle, M. ^{[2
]}

Butler, J. ^{[1
]}

Decostre, V. ^{[3
]}

Deborah, R. ^{[4
]}

Moraux, A. ^{[3
]}

Anthony, K. ^{[1
]}

Sleby, V. ^{[1
]}

Guglieri, M. ^{[2
]}

van der Holst, M. ^{[5
]}

Jansen, M. ^{[6
]}

Morgan, J. ^{[1
]}

de Groot, I. ^{[6
]}

Niks, E. ^{[5
]}

Verschuuren, J. ^{[5
]}

Servais, L. ^{[3
]}

Hogrel, J. Y. ^{[3
]}

Voit, T. ^{[3
]}

Straub, V. ^{[2
]}

Muntoni, F. ^{[1
]}

机构：

[1] UCL Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England

[2] Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

[3] Grp Hosp Pitie Salpetriere, Inst Myol, F-75634 Paris, France

[4] UCL Inst Child Hlth, Populat Policy & Practice Programme, London, England

[5] Leids Univ, Med Ctr, Leiden, Netherlands

[6] Radboud Univ Nijmegen, Med Ctr, NL-6525 ED Nijmegen, Netherlands

来源：

NEUROMUSCULAR DISORDERS | 2015年 / 25卷

关键词：

D O I：

10.1016/j.nmd.2015.06.162

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

G.P.147

引用

页码：S229 / S229

页数：1

共 50 条

[1] Outcome measures for Duchenne muscular dystrophy from ambulant to non-ambulant: implications for clinical trials
Domingos, J.
Eagle, M.
Moraux, A.
Butler, J.
Decostre, V.
Ridout, D.
Mayhew, A.
Selby, V.
Reguiba, N.
Guglieri, M.
Van der Holst, M.
Jansen, M.
Verschuuren, J. G. M.
de Groot, I.
Niks, E.
Servais, L.
Hogrel, J. Y.
Straub, V.
Voit, T.
Ricotti, V.
Muntoni, F.
[J]. NEUROMUSCULAR DISORDERS, 2016, 26 : S6 - S6
[2] Outcome measures for Duchenne muscular dystrophy from ambulant to non-ambulant: implications for clinical trials
Domingos, J.
Eagle, M.
Moraux, A.
Butler, J.
Decostre, V.
Ridout, D.
Mayhew, A.
Selby, V.
Guglieri, M.
Van der Holst, M.
Jansen, M.
Verschuuren, J. G. M.
de Groot, I.
Niks, E.
Servais, L.
Hogrel, J. Y.
Straub, V.
Voit, T.
Ricotti, V.
Muntoni, F.
[J]. NEUROMUSCULAR DISORDERS, 2017, 27 : S12 - S12
[3] Outcome measures for Duchenne muscular dystrophy from ambulant to non-ambulant: Implications for clinical trials
Domingos, J.
Eagle, M.
Moraux, A.
Butler, J.
Decostre, V.
Ridout, D.
Mayhew, A.
Selby, V.
Guglieri, M.
Van der Holst, M.
Jansen, M.
Verschuuren, J.
de Groot, I.
Niks, E.
Servais, L.
Hogrel, J. Y.
Straub, V.
Voit, T.
Ricotti, V.
Muntoni, F.
[J]. NEUROMUSCULAR DISORDERS, 2016, 26 : S185 - S185
[4] Outcome measures for Duchenne muscular dystrophy from ambulant to non-ambulant patients: implications for clinical trials
Domingos, J.
Eagle, M.
Moraux, A.
Butler, J.
Decostre, V.
Ridout, D.
Mayhew, A.
Selby, V.
Guglieri, M.
Van der Hoist, M.
Jansen, M.
Verschuuren, J.
de Groot, I.
Niks, E.
Servais, L.
Hogrel, J. Y.
Straub, V.
Voit, T.
Ricotti, V.
Muntoni, F.
[J]. NEUROMUSCULAR DISORDERS, 2017, 27 : S232 - S233
[5] Patient perception of outcome measures for non-ambulant Duchenne muscular dystrophy patients
Naarding, K.
Van der Holst, M.
Van de Velde, N.
Van Schaik-Bank, P.
Kan, H.
Niks, E.
[J]. NEUROMUSCULAR DISORDERS, 2019, 29 : S180 - S180
[6] Respiratory and upper limb function as outcome measures in ambulant and non-ambulant subjects with Duchenne muscular dystrophy: A prospective multicentre study
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Selby, V.
Ridout, D.
Domingos, J.
Decostre, V.
Mayhew, A.
Eagle, M.
Butler, J.
Guglieri, M.
Van der Holst, M.
Jansen, M.
Verschuuren, J. J. G. M.
de Groot, I. J. M.
Niks, E. H.
Servais, L.
Straub, V.
Voit, T.
Hogrel, J. Y.
Muntoni, F.
[J]. NEUROMUSCULAR DISORDERS, 2019, 29 (04) : 261 - 268
[7] Preserved thenar muscles in non-ambulant Duchenne muscular dystrophy patients
Naarding, Karin J.
Keene, Kevin R.
Sardjoe Mishre, Aashley S. D.
Veeger, Thom T. J.
van de Velde, Nienke M.
Prins, Arina J.
Burakiewicz, Jedrzej
Verschuuren, Jan J. G. M.
van der Holst, Menno
Niks, Erik H.
Kan, Hermien E.
[J]. JOURNAL OF CACHEXIA SARCOPENIA AND MUSCLE, 2021, 12 (03) : 694 - 703
[8] Respiratory involvement in ambulant and non-ambulant patients with facioscapulohumeral muscular dystrophy
Sandra Moreira
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[J]. Journal of Neurology, 2017, 264 : 1271 - 1280
[9] Respiratory involvement in ambulant and non-ambulant patients with facioscapulohumeral muscular dystrophy
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Wood, Libby
Smith, Debbie
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Muni-Lofra, Robert
Eglon, Gail
Williams, Maggie
Straub, Volker
Lochmuller, Hanns
Evangelista, Teresinha
[J]. JOURNAL OF NEUROLOGY, 2017, 264 (06) : 1271 - 1280
[10] The effect of corticosteroid on pulmonary function in non-ambulant adults with Duchenne muscular dystrophy
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Muni-Lofra, R.
Mayhew, A.
Waller, K.
Chapman, S.
Ramdharry, G.
Quinlivan, R.
[J]. NEUROMUSCULAR DISORDERS, 2021, 31 : S80 - S81

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